Trial Outcomes & Findings for Potential Impact of Patient Vitamin D Status in AK Response to MAL-PDT (NCT NCT02878382)

NCT ID: NCT02878382

Last Updated: 2020-08-04

Results Overview

To compare the efficacy of topical PDT alone versus Calcipotriol assisted PDT for AKs on the scalp. The values in the data table represent the mean (+sd) number of lesions on each side at 3, 6 and 12 months post intervention. Lesion counts include lesions that have not been cleared and also newly emerged lesions ( if new lesions emerge on the treated field) At baseline: number of AKs was 290 on the CAL-PDT side and 284 on the conventional side.

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

20 participants

Primary outcome timeframe

Change from baseline, 90 days, 180 days and 12 months after the PDT

Results posted on

2020-08-04

Participant Flow

All twenty patients completed the 12 -month study. Patients were male, Fitzpatrick skin types I-III and mean age 73.8 years (range 54-89).

Unit of analysis: half scalp

Participant milestones

Participant milestones
Measure
Calcipotriol Assisted MAL-PDT
Calcipotriol + MAL-PDT half scalp
Conventional MAL-PDT
MAL-PDT alone half scalp
Overall Study
STARTED
20 20
20 20
Overall Study
COMPLETED
20 20
20 20
Overall Study
NOT COMPLETED
0 0
0 0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Potential Impact of Patient Vitamin D Status in AK Response to MAL-PDT

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Participants
n=20 Participants
Conventional topical PDT with Methylaminolevulinate 16% in one half of the scalp with multiple AKs. Conventional MAL-PDT: Curettage of lesions and application of MAl cream 16% for 90 minutes under occlusion followed by LED 635 nm illumination at 37 J/cm2 total dose Calcipotriol ointment 50 mcg/g applied once a day for 15 consecutive days in one half of the scalp, before Conventional topical PDT Calcipotriol assisted MAL-PDT: Calcipotriol 50 mcg/g for 15 days prior to PDT. Curettage of lesions and application of MAl cream 16% for 90 minutes under occlusion followed by LED 635 nm illumination at 37 J/cm2 total dose
Age, Categorical
<=18 years
0 Participants
n=99 Participants
Age, Categorical
Between 18 and 65 years
5 Participants
n=99 Participants
Age, Categorical
>=65 years
15 Participants
n=99 Participants
Sex: Female, Male
Female
0 Participants
n=99 Participants
Sex: Female, Male
Male
20 Participants
n=99 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
Race (NIH/OMB)
Asian
0 Participants
n=99 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=99 Participants
Race (NIH/OMB)
White
20 Participants
n=99 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
Region of Enrollment
Brazil
20 participants
n=99 Participants
number of AKs at baseline
CAL-PDT side
290 number of lesions
n=99 Participants
number of AKs at baseline
Conventional PDT
284 number of lesions
n=99 Participants
number of AKs at baseline
CAL-PDT side grade I
223 number of lesions
n=99 Participants
number of AKs at baseline
CAL-PDT side grade II
67 number of lesions
n=99 Participants
number of AKs at baseline
Conventional PDT grade I
222 number of lesions
n=99 Participants
number of AKs at baseline
Conventional PDT grade II
62 number of lesions
n=99 Participants

PRIMARY outcome

Timeframe: Change from baseline, 90 days, 180 days and 12 months after the PDT

To compare the efficacy of topical PDT alone versus Calcipotriol assisted PDT for AKs on the scalp. The values in the data table represent the mean (+sd) number of lesions on each side at 3, 6 and 12 months post intervention. Lesion counts include lesions that have not been cleared and also newly emerged lesions ( if new lesions emerge on the treated field) At baseline: number of AKs was 290 on the CAL-PDT side and 284 on the conventional side.

Outcome measures

Outcome measures
Measure
Calcipotriol Assisted MAL-PDT
n=20 Participants
Calcipotriol 15 days before - once a day intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Conventional MAL-PDT
n=20 Participants
intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Changes From Baseline in Actinic Keratosis - Lesion Base Count.
3 months outcome
1.15 lesions
Standard Deviation 0.99
2.65 lesions
Standard Deviation 1.35
Changes From Baseline in Actinic Keratosis - Lesion Base Count.
6 months outcome
1.15 lesions
Standard Deviation 0.93
2.60 lesions
Standard Deviation 1.14
Changes From Baseline in Actinic Keratosis - Lesion Base Count.
12 months outcome
1.35 lesions
Standard Deviation 1.04
3.20 lesions
Standard Deviation 1.44

PRIMARY outcome

Timeframe: Change from baseline, 90 days, 6 months and 12 months after PDT

AK clearance after PDT and comparison between the sides The values in the data table represent the percentage of AK clearance on each side at 3, 6 and 12 months post intervention. At baseline: 290 on the CAL-PDT side and 284 on the conventional side.

Outcome measures

Outcome measures
Measure
Calcipotriol Assisted MAL-PDT
n=20 Participants
Calcipotriol 15 days before - once a day intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Conventional MAL-PDT
n=20 Participants
intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Percentage of Actinic Keratosis (AK) Lesions Cleared
3 months outcome
92.1 percentage of lesions cleared
82 percentage of lesions cleared
Percentage of Actinic Keratosis (AK) Lesions Cleared
6 months outcome
92.1 percentage of lesions cleared
81.7 percentage of lesions cleared
Percentage of Actinic Keratosis (AK) Lesions Cleared
12 months outcome
90.7 percentage of lesions cleared
77.5 percentage of lesions cleared

SECONDARY outcome

Timeframe: immediately after intervention

Measurement of pain during LED illumination and comparison between the sides with a visual analogue scale (VAS), considering 0 as absence of pain and 10 as the most severe pain. At baseline, before the illumination, there is an absence of pain, which means Score 0 (zero) for all participants before the procedure. Pain is reffered during and after the illumination and measured with the VAS scale, reported by each patient.

Outcome measures

Outcome measures
Measure
Calcipotriol Assisted MAL-PDT
n=20 Participants
Calcipotriol 15 days before - once a day intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Conventional MAL-PDT
n=20 Participants
intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Pain Scores Immediately Post Illumination
5.4 units on a scale
Standard Deviation 1.4
4.0 units on a scale
Standard Deviation 0.69

SECONDARY outcome

Timeframe: Baseline and 10 minutes after illumination

Measurement of PPIX fluorescence on both sides of the scalp before and immediately after LED illumination PpIX fluorescence was measured in three different spot areas on the scalp before and immediately after PDT on each side. The measurements were taken noninvasively in the areas where PpIX fluorescence was more intense, with a handheld fluorescence photometer (USB 2000+ spectroscopy device; Ocean Optics, Dunedin, FL, U.S.A.). The photometer illuminates a circular skin area with a diameter of 1 cm with blue light (400-420 nm), matching the Soret band of PpIX at 405-420 nm. By measuring excitation wavelengths at 600- 700 nm, the corresponding red PpIX fluorescence intensity at 633 nm is detected. Measurements were taken in arbitrary units. The mean PpIX fluorescence value for each side was calculated before and after the treatment.

Outcome measures

Outcome measures
Measure
Calcipotriol Assisted MAL-PDT
n=20 Participants
Calcipotriol 15 days before - once a day intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Conventional MAL-PDT
n=20 Participants
intervention: MAL-PDT plus curettage Illumination LED 635 nm 37J/cm2
Change From Baseline in Fluorescence Intensity of PPIX
3422.85 arbitrary units
Standard Deviation 1775.19
2688.35 arbitrary units
Standard Deviation 1746.12

Adverse Events

Calcipotriol Assisted MAL-PDT

Serious events: 0 serious events
Other events: 15 other events
Deaths: 0 deaths

Conventional MAL-PDT

Serious events: 0 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Calcipotriol Assisted MAL-PDT
n=20 participants at risk
Calcipotriol ointment 50 mcg/g applied once a day for 15 consecutive days in one half of the scalp, before Conventional topical PDT Calcipotriol assisted MAL-PDT: Calcipotriol 50 mcg/g for 15 days prior to PDT. Curettage of lesions and application of MAl cream 16% for 90 minutes under occlusion followed by LED 635 nm illumination at 37 J/cm2 total dose
Conventional MAL-PDT
n=20 participants at risk
Conventional topical PDT with Methylaminolevulinate 16% in one half of the scalp with multiple AKs. Conventional MAL-PDT: Curettage of lesions and application of MAl cream 16% for 90 minutes under occlusion followed by LED 635 nm illumination at 37 J/cm2 total dose
Skin and subcutaneous tissue disorders
local skin reactions
75.0%
15/20 • Number of events 22 • side effects collected over 10 days
During light exposure patients were asked to evaluate the intensity of pain using a visual analogue scale (VAS), considering 0 as absence of pain and 10 as the most severe pain. Local skin reactions (erythema, edema, pustules, crusts, erosions and ulcerations) were recorded as well as any systemic adverse events during treatment and after follow-up visits. Clinical assessments of the local skin reactions were performed on a pre-defined scale as: 0 = no reaction, + mild, ++ moderate, +++ severe
60.0%
12/20 • Number of events 20 • side effects collected over 10 days
During light exposure patients were asked to evaluate the intensity of pain using a visual analogue scale (VAS), considering 0 as absence of pain and 10 as the most severe pain. Local skin reactions (erythema, edema, pustules, crusts, erosions and ulcerations) were recorded as well as any systemic adverse events during treatment and after follow-up visits. Clinical assessments of the local skin reactions were performed on a pre-defined scale as: 0 = no reaction, + mild, ++ moderate, +++ severe

Additional Information

Dr Luis Torezan Associate Professor Dermatology

University of Sao Paulo Medical School Brazil

Phone: +551138491888

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place