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Expanded Access for Lorenzo's Oil (GTO/GTE) in Adrenoleukodystrophy

NCT02233257 · Status: NO_LONGER_AVAILABLE · Type: EXPANDED_ACCESS

Last updated 2018-01-23

No results posted yet for this study

Summary

X-linked adrenoleukodystrophy (ALD) is a genetic disorder affecting the brain and adrenal glands. Approximately one third of boys who are at risk will develop cerebral disease. Using a specific diet and the compound Lorenzo's oil, it can be shown that very long chain fatty acids may be lowered in the blood, but it is not known to what degree that may prevent the onset of childhood disease.

This proposal makes available Lorenzo's oil to individuals with ALD, a life threatening disorder for which there are presently no other therapies.

Conditions

  • X-linked Adrenoleukodystrophy

Interventions

DRUG

Lorenzo's Oil

Oral use of Lorenzo's oil to lower very long chain fatty acids

Sponsors & Collaborators

Principal Investigators

  • Gerald V Raymond, MD · University of Minnesota

Eligibility

Min Age
18 Months
Max Age
18 Years
Sex
MALE
Healthy Volunteers
No

Timeline & Regulatory

Countries

  • United States

Study Locations

More Related Trials

Entities

Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT02233257 on ClinicalTrials.gov