A Study of Respiratory Muscle Strength in Patients With Late-onset Pompe Disease (LOPD)

NCT02191917 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 8

Last updated 2023-01-09

Study results available
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Summary

Study 701-201 is a study in patients with late-onset Pompe disease (LOPD). The study will test respiratory muscle strength initially and again after 24 weeks in subjects treated or not treated with BMN 701 .

Conditions

  • Late-onset Pompe Disease

Interventions

PROCEDURE

Respiratory muscle strength measurements by different techniques.

Sponsors & Collaborators

Principal Investigators

  • Medical Monitor, MD · BioMarin Pharmaceutical

Eligibility

Min Age
18 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2014-10-21
Primary Completion
2016-06-22
Completion
2016-06-22

Countries

  • United States
  • United Kingdom

Study Locations

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Entities

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT02191917 on ClinicalTrials.gov