A Study of Respiratory Muscle Strength in Patients With Late-onset Pompe Disease (LOPD)
NCT02191917 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 8
Last updated 2023-01-09
Summary
Study 701-201 is a study in patients with late-onset Pompe disease (LOPD). The study will test respiratory muscle strength initially and again after 24 weeks in subjects treated or not treated with BMN 701 .
Conditions
- Late-onset Pompe Disease
Interventions
- PROCEDURE
-
Respiratory muscle strength measurements by different techniques.
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Medical Monitor, MD · BioMarin Pharmaceutical
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2014-10-21
- Primary Completion
- 2016-06-22
- Completion
- 2016-06-22
Countries
- United States
- United Kingdom
Study Locations
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