Post Study Continuation of C7 for G1D
NCT02018302 · Status: NO_LONGER_AVAILABLE · Type: EXPANDED_ACCESS
Last updated 2019-04-18
Summary
This protocol provides ongoing access to triheptanoin for patients who did complete an initial pilot protocol, and provides the opportunity to collect long-term safety data from patients treated with triheptanoin.
Conditions
- Glut1 Deficiency Syndrome
- Glucose Transporter Type 1 Deficiency Syndrome
Interventions
- DRUG
-
Triheptanoin
Sponsors & Collaborators
-
Juan Pascual
lead OTHER
Principal Investigators
-
Juan M Pascual, MD, PhD · UT Southwestern Medical Center
Eligibility
- Min Age
- 1 Month
- Max Age
- 28 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
Countries
- United States
Study Locations
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