Treatment Use of 3,4-Diaminopyridine
NCT01765140 · Status: NO_LONGER_AVAILABLE · Type: EXPANDED_ACCESS
Last updated 2025-01-20
Summary
This protocol provided 3,4 diaminopyridine (DAP) under a treatment-use IND to patients with congenital myasthenic syndrome (CMS). It is now closed.
Conditions
- Myasthenic Syndromes, Congenital
Interventions
- DRUG
-
3,4-diaminopyridine
Treatment use of 3,4-DAP for patients with congenital myasthenic syndrome (CMS)
Sponsors & Collaborators
-
Vern C. Juel, M.D.
lead OTHER
Principal Investigators
-
Vern C. Juel, M.D. · Duke University
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
Countries
- United States
Study Locations
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