Skin and Blood Research Samples From Healthy Volunteers and Patients With Hematologic Diseases
NCT00840567 · Status: TERMINATED · Phase: NA · Type: INTERVENTIONAL · Enrollment: 7
Last updated 2013-07-11
Summary
The investigators plan to obtain skin and blood samples from healthy volunteers and patients with a benign, inherited hematologic disease to use for research to use homologous recombination to correct β-globin gene mutations in therapeutically useful cells, like autologous induced pluripotent stem cells from sickle cell anemia patients.
Conditions
- Anemia, Sickle Cell
Interventions
- PROCEDURE
-
Skin biopsy
- PROCEDURE
-
Blood draw & sample
Sponsors & Collaborators
-
Washington University School of Medicine
lead OTHER
Principal Investigators
-
Timothy Ley, M.D. · Washington Univerisity School of Medicine
Study Design
- Allocation
- NON_RANDOMIZED
- Purpose
- BASIC_SCIENCE
- Masking
- NONE
- Model
- PARALLEL
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- Yes
Timeline & Regulatory
- Start
- 2009-02-28
- Primary Completion
- 2010-10-31
- Completion
- 2010-10-31
Countries
- United States
Study Locations
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