Autologous Stem Cell Transplant for Neurologic Autoimmune Diseases

NCT00716066 · Status: ACTIVE_NOT_RECRUITING · Phase: PHASE2 · Type: INTERVENTIONAL · Enrollment: 53

Last updated 2026-02-27

No results posted yet for this study

Summary

This phase II trial studies the side effects and how well carmustine, etoposide, cytarabine and melphalan together with antithymocyte globulin before a stem cell transplant works in treating patients with autoimmune neurologic disease that did not respond to previous therapy. In autoimmune neurological diseases, the patient's own immune system 'attacks' the nervous system which might include the brain/spinal cord and/or the peripheral nerves. Giving high-dose chemotherapy, including carmustine, etoposide, cytarabine, melphalan, and antithymocyte globulin, before a stem cell transplant weakens the immune system and may help stop the immune system from 'attacking' a patient's nervous system. When the patient's own (autologous) stem cells are infused into the patient they help the bone marrow make red blood cells, white blood cells, and platelets so the blood counts can improve.

Conditions

  • Autoimmune Disease
  • Neurologic Autoimmune Disease
  • Autologous Transplant Autoimmune
  • Multiple Sclerosis Transplant
  • MS Stem Cell Transplant
  • Multiple Sclerosis Stem Cell Transplant
  • Stiff Person Syndrome
  • HCT for Neurologic Autoimmune Disorders
  • CIDP Transplant
  • Myasthenia Gravis Transplant
  • Autoimmune Nervous System Disorder
  • Central Nervous System Vasculitis
  • Cerebellar Degeneration
  • Chronic Inflammatory Demyelinating Polyneuropathy
  • Lambert Eaton Myasthenic Syndrome
  • Myasthenia Gravis
  • Neuromyelitis Optica
  • Opsoclonus Myoclonus Syndrome
  • Rasmussen Subacute Encephalitis

Interventions

BIOLOGICAL

Anti-Thymocyte Globulin

Given IV

PROCEDURE

Autologous Hematopoietic Stem Cell Transplantation

Undergo autologous or syngeneic stem cell transplantation

DRUG

Carmustine

Given IV

DRUG

Cytarabine

Given IV

DRUG

Etoposide

Given IV

OTHER

Laboratory Biomarker Analysis

Correlative studies

DRUG

Melphalan

Given IV

PROCEDURE

Peripheral Blood Stem Cell Transplantation

Undergo autologous or syngeneic stem cell transplantation

DRUG

Prednisone

Given PO

PROCEDURE

Syngeneic Bone Marrow Transplantation

Undergo syngeneic bone marrow transplantation

Sponsors & Collaborators

  • Fred Hutchinson Cancer Center

    lead OTHER

Principal Investigators

  • Leona Holmberg · Fred Hutch/University of Washington Cancer Consortium

Study Design

Allocation
NA
Purpose
TREATMENT
Masking
NONE
Model
SINGLE_GROUP

Eligibility

Max Age
71 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2008-06-30
Primary Completion
2025-12-30
Completion
2030-01-31

Countries

  • United States

Study Locations

More Related Trials

Entities

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT00716066 on ClinicalTrials.gov