Bezafibrate Trial in CPT2 Deficiency
NCT00336167 · Status: UNKNOWN · Phase: PHASE3 · Type: INTERVENTIONAL · Enrollment: 12
Last updated 2007-04-09
Summary
The purpose of this study is to determine whether bezafibrate is effective in the treatment of the muscular adult form of carnitine palmitoyltransferase 2 deficiency
Conditions
- Carnitine Palmitoyl Transferase 2 Deficiency
Interventions
- DRUG
-
bezafibrate (drug)
Sponsors & Collaborators
-
Association Française contre les Myopathies (AFM), Paris
collaborator OTHER -
Institut National de la Santé Et de la Recherche Médicale, France
collaborator OTHER_GOV -
Assistance Publique - Hôpitaux de Paris
lead OTHER
Principal Investigators
-
Bruno EYMARD, M.D · Service de Neurologie 2 Groupe hospitalier Pitié-Salpétriere, Paris, France
-
Jean Paul BONNEFONT, M.D., Ph D, · Unite INSERM U781
Study Design
- Allocation
- NON_RANDOMIZED
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2006-06-30
- Completion
- 2007-07-31
Countries
- France
Study Locations
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