GTA-Glyceryltriacetate for Canavan Disease
NCT00278707 · Status: UNKNOWN · Phase: PHASE1 · Type: INTERVENTIONAL · Enrollment: 5
Last updated 2006-08-15
Summary
The purpose of this study is to determine whether oral supplementation of glyceryl triacetate improves the clinical prognosis of Canavan Disease.
Conditions
- Infantile Canavan Disease
- Deficiency Disease, Aspartoacylase
Interventions
- DRUG
-
GTA: Glyceryltriacetate
Sponsors & Collaborators
-
Sheba Medical Center
lead OTHER_GOV
Principal Investigators
-
Yair Anikster, MD PI · Director Metabolic Disease Unit
Study Design
- Allocation
- NON_RANDOMIZED
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Min Age
- 0 Years
- Max Age
- 15 Months
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2006-01-31
- Completion
- 2006-07-31
Countries
- Israel
Study Locations
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