Phase III Study of L-Cysteine in Patients With Erythropoietic Protoporphyria

N-Acetylcysteine in Patients With Sickle Cell Disease

NCT01849016 ·Status: COMPLETED ·Phase: PHASE3

A Study of the Absorption, Metabolism, and Excretion of GBT440 in Healthy Male Subjects

NCT02497924 ·Status: COMPLETED ·Phase: PHASE1

A Study to Evaluate Safety, Pharmacokinetic, and Biological Activity of INCB059872 in Subjects With Sickle Cell Disease

NCT03132324 ·Status: TERMINATED ·Phase: PHASE1

Study of the Efficacy and Safety of Parsaclisib in Participants With Primary Warm Autoimmune Hemolytic Anemia

NCT05073458 ·Status: TERMINATED ·Phase: PHASE3

Erythropoietic Protoporphyrias: Studies of the Natural History, Genotype-Phenotype Correlations, and Psychosocial Impact

NCT01688895 ·Status: COMPLETED

Does Exercise and Heat Increase the Lightsensibility in Patients With Erythropoietic Protoporphyria

NCT00206869 ·Status: UNKNOWN ·Phase: NA

PK and PD Responses to Oral L-Citrulline in Patients With Sickle Cell Disease

NCT00343954 ·Status: UNKNOWN ·Phase: PHASE1

Phase II Randomized Trial:Arginine Butyrate Plus Standard Local Therapy in Patients With Refractory Sickle Cell Ulcers

NCT00004412 ·Status: COMPLETED ·Phase: PHASE2

Study of High-Dose Pulse Administration DN-101 (Calcitriol) in Patients With Myelodysplastic Syndrome (MDS)

NCT00057031 ·Status: UNKNOWN ·Phase: PHASE2

Studies in Porphyria III: Heme and Tin Mesoporphyrin in Acute Porphyrias

NCT00004396 ·Status: COMPLETED ·Phase: PHASE2

Dose-Escalation Study of SCD-101 in Sickle Cell Disease

NCT02380079 ·Status: UNKNOWN ·Phase: PHASE1

Oral Iron for Erythropoietic Protoporphyrias

NCT02979249 ·Status: COMPLETED ·Phase: NA

Phase III Randomized Study of Poloxamer 188 for Vaso-Occlusive Crisis of Sickle Cell Disease

NCT00004408 ·Status: COMPLETED ·Phase: PHASE3

A Study of the Effect of IW-1701 (Olinciguat), a Stimulator of Soluble Guanylate Cyclase (sGC), on Patients With Sickle Cell Disease (SCD)

NCT03285178 ·Status: COMPLETED ·Phase: PHASE2

Antioxidant Therapy to Reduce Inflammation in Sickle Cell Disease

NCT01054768 ·Status: COMPLETED ·Phase: PHASE2

Iron Therapy in Erythropoietic Protoporphyria

NCT05572125 ·Status: COMPLETED

A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease

NCT04987489 ·Status: COMPLETED ·Phase: PHASE2

Phase I Study of Tin Mesoporphyrin in Patients on Long Term Heme Therapy for Prevention of Acute Attacks of Porphyria

NCT00004397 ·Status: COMPLETED ·Phase: PHASE1

Clinical Study of BRL-101 in the Treatment of Sickle Cell Disease

NCT06287099 ·Status: NOT_YET_RECRUITING ·Phase: NA

Study to Determine the Safety and Tolerability of Sotatercept (ACE-011) in Adults With Beta( β)- Thalassemia.

NCT01571635 ·Status: TERMINATED ·Phase: PHASE2

Improvement of Fatigue Symptoms in the Iron Deficiency Anemia With Iron Succinylate Therapy

NCT03873584 ·Status: WITHDRAWN

Light Exposure Patterns and Symptoms Among Patients With Erythropoietic Protoporphyria

NCT03682731 ·Status: COMPLETED

A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia

NCT05664737 ·Status: RECRUITING ·Phase: PHASE2

Intravenous Iron in Adults With Cystic Fibrosis

NCT03632525 ·Status: COMPLETED ·Phase: PHASE4

Panhematin for Prevention of Acute Attacks of Porphyria

NCT02922413 ·Status: TERMINATED ·Phase: PHASE2