Phase II Study of Ribose, Uridine, and Thymidine for a Complex Syndrome Involving Excessive 5'-Nucleotidase Activity
NCT00004658 · Status: COMPLETED · Phase: PHASE2 · Type: INTERVENTIONAL
Last updated 2005-06-24
Summary
OBJECTIVES: I. Evaluate the efficacy of oral ribose in patients with a complex 5'-nucleotidase syndrome who have not received uridine (UR) and thymidine (TDR).
II. Evaluate the efficacy of UR/oral ribose and UR/TDR. III. Evaluate the efficacy of oral ribose given in combination with UR/TDR.
Conditions
- 5'-Nucleotidase Syndrome
Interventions
- DRUG
-
ribose
- DRUG
-
thymidine
- DRUG
-
uridine
Sponsors & Collaborators
-
University of California, San Diego
collaborator OTHER -
National Center for Research Resources (NCRR)
lead NIH
Principal Investigators
-
Alice L. Yu · University of California, San Diego
Study Design
- Purpose
- TREATMENT
Eligibility
- Min Age
- 0 Years
- Max Age
- 21 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 1995-03-31
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