News Related to ABCA4

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Ocugen Completes Enrollment in Pivotal Stargardt Disease Gene Therapy Study

Apr 03, 2026

Ocugen has completed enrollment and dosing in its phase II/III GARDian3 study for OCU410ST gene therapy targeting Stargardt disease. The study includes 63 patients and aims to address over 1,200 ABCA4 gene mutations with a single treatment. Interim data is expected in Q3 2026, with a BLA submission targeted for mid-2027.