News Related to Kalydeco

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Biotech Investors Eye Cystic Fibrosis Trials and Rare-Disease Drugs

Apr 05, 2026

Biotech investors are closely watching cystic fibrosis drug trials, rare-disease therapies and regulatory catalysts. Sionna Therapeutics is advancing a new CF drug class, while Praxis Precision Medicines targets essential tremor. FDA staffing challenges add uncertainty to approval timelines.

CRISPR Therapeutics Positioned for Growth as Casgevy Sales Rise

Feb 20, 2026

Switzerland-based CRISPR Therapeutics stands to benefit from increased Casgevy sales following partner Vertex Pharmaceuticals' fourth-quarter results, with five additional gene-editing therapies in clinical trials targeting larger patient populations.