Gene-Modified Stem Cell Therapy for Subjects With Transfusion-dependent Beta-thalassemia
- Status
- RECRUITING
- Phase
- PHASE2
Clinical Trials Related to Transfusion-dependent Beta-Thalassemia
Related studies linked through entity extraction aliases.
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
- Status
- RECRUITING
- Phase
- PHASE3
Use of the Hemanext One® Hypoxic Red Blood Cell Storage System for Transfusion in Thalassemia Patients
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
Plasticizer Exposure and Its Consequences on Health
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
Β-Thalassemia Treatment with KL003 Cell Injection
- Status
- RECRUITING
- Phase
- PHASE1/PHASE2
Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients
- Status
- RECRUITING
- Phase
- NA
Deciphering Effects of Thalidomide on Red Blood Cells in Transfusion Dependents Beta Thalassemia Patients
- Status
- COMPLETED
- Phase
- PHASE3
Growth and Development-related Outcomes in Children With Transfusion-dependent Beta-thalassemia After Gene Therapy
- Status
- RECRUITING
- Phase
- N/A
Evaluation the Safety and Efficacy of KL003 Cell Injection in the Treatment of Transfusion-dependent β-thalassemia.
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- NA
A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE3
Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- N/A