NCT04443907 Study of Safety and Efficacy of Genome-edited Hematopoietic Stem and Progenitor Cells in Sickle Cell Disease (SCD) Status TERMINATED Phase PHASE1
NCT04432623 The BENeFiTS Trial in Beta Thalassemia Intermedia Status ENROLLING_BY_INVITATION Phase PHASE1/PHASE2
NCT04416178 Sickle Cell Disease and the Genomic and Gene Therapy Needs of Stakeholders Status RECRUITING Phase N/A
NCT04398628 ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders Status RECRUITING Phase N/A
NCT04388241 Preliminary Feasibility and Efficacy of Behavioral Intervention to Reduce Pain-Related Disability in Pediatric SCD Status COMPLETED Phase NA
NCT04380610 Improving Scientific Rigor of Renal Clinical Endpoints for Sickle Cell Anemia Status COMPLETED Phase N/A
NCT04362293 Reduced Intensity Transplantation for Severe Sickle Cell Disease Status SUSPENDED Phase PHASE2
NCT04349189 Venous Thrombosis Biomarkers in Sickle Cell Disease and Sickle Cell Trait Status COMPLETED Phase N/A
NCT04335721 A Voxelotor for Sickle Cell Anemia Patients at Highest Risk for Progression of Chronic Kidney Disease Status TERMINATED Phase PHASE1/PHASE2
NCT04301336 Different Treatment Modalities in the Management of the Painful Crisis in Pediatric Sickle- Cell Anemia Status COMPLETED Phase PHASE2/PHASE3
NCT04293185 A Study Evaluating Gene Therapy With BB305 Lentiviral Vector in Sickle Cell Disease Status ACTIVE_NOT_RECRUITING Phase PHASE3
NCT04293172 Study to Evaluate the Effect of Ticagrelor Versus Placebo in Reducing Vaso-Occlusive Crises Rate in Pediatric Patients With Sickle Cell Disease. Status WITHDRAWN Phase PHASE3
NCT04289311 SMYLS: A Self-management Program for Youth Living With Sickle Cell Disease Status COMPLETED Phase NA