The International PNH Interest Group PNH Registry
- Status
- RECRUITING
- Phase
- N/A
Clinical Trials Related to Paroxysmal Nocturnal Hemoglobinuria
Related studies linked through entity extraction aliases.
Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis
- Status
- RECRUITING
- Phase
- PHASE3
MT2023-20: Hematopoietic Cell Transplant With Reduced Intensity Conditioning and Post-transplant Cyclophosphamide for Severe Aplastic Anemia and Other Forms of Acquired Bone Marrow Failure.
- Status
- RECRUITING
- Phase
- PHASE2
Home Reported Outcomes in PNH
- Status
- RECRUITING
- Phase
- N/A
A Study to Test if SAR443809 is Tolerated and Safe When Taken as a Single Dose in Healthy Adults
- Status
- COMPLETED
- Phase
- PHASE1
Long-Term Safety, Tolerability and Efficacy of OMS906 in Paroxysmal Nocturnal Hemoglobinuria
- Status
- RECRUITING
- Phase
- PHASE2
Long-term Safety and Tolerability of HRS-5965 in Patients With Paroxysmal Nocturnal Hemoglobinuria
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE2
A Real-world, Multi-center, Prospective, Observational Study for PNH in China
- Status
- COMPLETED
- Phase
- N/A
Dose Escalation of BCX10013 in Participants with Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Status
- COMPLETED
- Phase
- PHASE1
Proof of Concept Study to Assess the Efficacy, Safety of HRS-5965 in Patients With Paroxysmal Nocturnal Hemoglobinuria
- Status
- COMPLETED
- Phase
- PHASE2
A Study of MY008211A in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Status
- COMPLETED
- Phase
- PHASE2
Compassionate Use of Pozelimab and Cemdisiran Combination Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria
- Status
- NO_LONGER_AVAILABLE
- Phase
- N/A
Danicopan Early Access Program
- Status
- AVAILABLE
- Phase
- N/A
Safety and Efficacy of OMS906 in Paroxysmal Nocturnal Hemoglobinuria Patients With a Sub-optimal Response to Ravulizumab
- Status
- COMPLETED
- Phase
- PHASE2
Study of the Safety and Efficacy of OMS906 in Patients With Paroxysmal Nocturnal Hemoglobinuria
- Status
- COMPLETED
- Phase
- PHASE1
Eculizumab in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) in China
- Status
- COMPLETED
- Phase
- PHASE3
Hematological Response in Patients With Paroxysmal Nocturnal Hemoglobinuria Treated With Anti-C5 Antibody: an External Control Arm Study for Iptacopan Use in Anti-C5 naïve Patients
- Status
- COMPLETED
- Phase
- N/A
Effect of Food on Pharmacokinetics of MY008211A Tablets in Healthy Adult Subjects
- Status
- COMPLETED
- Phase
- PHASE1
A Study of Multiple Ascending Doses MY008211A in Healthy Adults
- Status
- COMPLETED
- Phase
- PHASE1
A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Status
- RECRUITING
- Phase
- N/A