An Extension Study to Assess the Long-term Safety and Efficacy of Hunterase (Idursulfase Beta)
- Status
- COMPLETED
- Phase
- PHASE3
Clinical Trials Related to MPS II
Related studies linked through entity extraction aliases.
RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome)
- Status
- SUSPENDED
- Phase
- PHASE3
MPS II Immunophenotyping
- Status
- TERMINATED
- Phase
- N/A
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
- Status
- RECRUITING
- Phase
- PHASE1
Longitudinal Study of Neurodegenerative Disorders
- Status
- RECRUITING
- Phase
- N/A
Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-913 in Subjects With MPS II
- Status
- TERMINATED
- Phase
- PHASE1/PHASE2
Safety and Clinical Outcomes in Hunter Syndrome Patients 5 Years of Age and Younger Receiving Idursulfase Therapy
- Status
- COMPLETED
- Phase
- PHASE4