BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
- Status
- NO_LONGER_AVAILABLE
- Phase
- N/A
Clinical Trials Related to Hurler Syndrome
Related studies linked through entity extraction aliases.
RGX-111 Gene Therapy in Patients With MPS I
- Status
- SUSPENDED
- Phase
- PHASE1/PHASE2
Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE2
Bone Marrow Transplant With Abatacept for Non-Malignant Diseases
- Status
- COMPLETED
- Phase
- PHASE1
Neurobehavioral Phenotypes in MPS III
- Status
- COMPLETED
- Phase
- N/A
Laronidase (Aldurazyme TM) Enzyme Replacement Therapy With Hematopoietic Stem Cell Transplant for Hurler Syndrome
- Status
- TERMINATED
- Phase
- N/A
Administration of IV Laronidase Post Bone Marrow Transplant in Hurler
- Status
- COMPLETED
- Phase
- PHASE1
Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders
- Status
- COMPLETED
- Phase
- PHASE2
Intrathecal Enzyme Replacement for Hurler Syndrome
- Status
- COMPLETED
- Phase
- PHASE1
Effects of Growth Hormone in Chronically Ill Children
- Status
- WITHDRAWN
- Phase
- NA
Study of Aldurazyme® Replacement Therapy in Patients With Mucopolysaccharidosis I (MPS I) Disease
- Status
- COMPLETED
- Phase
- PHASE3
Stem Cell Transplant w/Laronidase for Hurler
- Status
- COMPLETED
- Phase
- PHASE2
A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Less Than 5 Years Old
- Status
- COMPLETED
- Phase
- PHASE2