An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry Disease
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE1/PHASE2
Clinical Trials Related to Fabry Disease
Related studies linked through entity extraction aliases.
A Long Term Follow-Up Study of Fabry Disease Subjects Treated With FLT190
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Long Duration Holter ECG in Fabry Disease
- Status
- RECRUITING
- Phase
- NA
A Study to Describe the Experience of Both Patients and Their Clinicians in the Treatment of Fabry Disease With Enzyme Replacement Therapy.
- Status
- COMPLETED
- Phase
- N/A
A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- Status
- RECRUITING
- Phase
- N/A
Complement Activation in the Lysosomal Storage Disorders
- Status
- WITHDRAWN
- Phase
- N/A
Screening of Fabry Disease in Patients With GI Symptoms
- Status
- UNKNOWN
- Phase
- N/A
To Assess the Glycosphingolipid Clearance and Clinical Effects of Switching to Agalsidase Beta (Fabrazyme) Versus Continuing on Agalsidase Alfa (Replagal) in Male Patients With Classic Fabry Disease
- Status
- WITHDRAWN
- Phase
- PHASE4
Study of the Spermatic Characteristics of Patients With Fabry Disease
- Status
- COMPLETED
- Phase
- NA
Therapeutic Exercise to Treat Neuropathic Pain
- Status
- COMPLETED
- Phase
- NA
Safety, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged >12 Years) With Fabry Disease
- Status
- COMPLETED
- Phase
- PHASE3
Dose-Ranging Study of ST-920, an AAV2/6 Human Alpha Galactosidase A Gene Therapy in Subjects With Fabry Disease (STAAR)
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Treatment-related Benefit and Satisfaction in Fabry Patients. Insight in Patients Expectations and Preferences
- Status
- COMPLETED
- Phase
- N/A
A Fabry Disease Gene Therapy Study
- Status
- TERMINATED
- Phase
- PHASE1/PHASE2
Heidelberg In Vivo Confocal Microscopy to Evaluate the Ocular Surface Disorders of Healthy and Diseased Individuals
- Status
- UNKNOWN
- Phase
- N/A
A Study to Evaluate Migalastat in Fabry Subjects With Amenable GLA Variant and Renal Disease
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE3
A Study of Migalastat in Fabry Disease
- Status
- UNKNOWN
- Phase
- N/A
Screening for Fabry Disease in Renal Transplantation
- Status
- TERMINATED
- Phase
- N/A
Effect of Migalastat on Cardiac Involvement in Fabry Disease
- Status
- COMPLETED
- Phase
- N/A
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE3