German Observational Multicenter Study of Patients With Fabry Disease Under Chaperone Therapy With Migalastat-HCl.
- Status
- COMPLETED
- Phase
- N/A
Clinical Trials Related to Fabry Disease
Related studies linked through entity extraction aliases.
Study of the Relation Between Lipid Myocardial Overload Evaluated by Cardiac Magnetic Resonance Imaging (MRI), Alteration of Longitudinal Myocardial Deformations by Echocardiography, and Clinical Achievements (Functional, Biological and Electrical) in Fabry Disease, and Its Outcomes.
- Status
- UNKNOWN
- Phase
- N/A
Safety and Efficacy of PRX-102 in Patients With Fabry Disease Currently Treated With REPLAGAL® (Agalsidase Alfa)
- Status
- COMPLETED
- Phase
- PHASE3
Pharmacokinetics, Pharmacodynamics, and Safety of Moss-aGalactosidase A in Patients With Fabry Disease
- Status
- COMPLETED
- Phase
- PHASE1
Podocyturia - Predictor of Renal Dysfunction in Fabry Nephropathy
- Status
- UNKNOWN
- Phase
- N/A
Assessment of Small Fiber Neuropathy in Rare Diseases Using Sudoscan
- Status
- COMPLETED
- Phase
- NA
Fabry: Renal Function During Long-term ERT by 51Cr-EDTA Clearance
- Status
- COMPLETED
- Phase
- N/A
A Study to Assess the Safety and Tolerability of Lucerastat in Subjects With Fabry Disease
- Status
- COMPLETED
- Phase
- PHASE1
Study to Evaluate the Safety and EffIcacy of PRX-102 on Gastrointestinal Symptoms in Naïve Fabry Disease
- Status
- WITHDRAWN
- Phase
- PHASE3
Cardiac Involvement in Adult Patients With Fabry Disease; Relation to Enzyme Replacement Therapy
- Status
- COMPLETED
- Phase
- N/A
Fabry Disease in Cerebrovascular Disease
- Status
- UNKNOWN
- Phase
- N/A
Study of the Prevalence of Fabry Disease in French Dialysis Patients
- Status
- UNKNOWN
- Phase
- N/A
Autologous Stem Cell Transplantation of Cells Engineered to Express Alpha-Galactosidase A in Patients With Fabry Disease
- Status
- COMPLETED
- Phase
- PHASE1
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
- Status
- COMPLETED
- Phase
- PHASE3
Lipidomics and Functional Analyses of Platelets in Fabry Disease
- Status
- UNKNOWN
- Phase
- N/A
Evaluation of the Long-term Safety, Pharmacodynamics, and Exploratory Efficacy of GZ/SAR402671 in Treatment-Naïve Adult Male Patients With Fabry Disease
- Status
- COMPLETED
- Phase
- PHASE2
Evaluate the Safety, Pharmacodynamics, Pharmacokinetics, and Exploratory Efficacy of GZ/SAR402671 in Treatment-naïve Adult Male Patients With Fabry Disease
- Status
- COMPLETED
- Phase
- PHASE2
Open-Label Extension Study of the Long-Term Effects of Migalastat HCL in Patients With Fabry Disease
- Status
- COMPLETED
- Phase
- PHASE3
Screening for Fabry Disease in a Pediatric Population at Risk
- Status
- COMPLETED
- Phase
- N/A
Investigating Lysosomal Storage Diseases in Minority Groups
- Status
- UNKNOWN
- Phase
- N/A