Gene Therapy for Alpha 1- Antitrypsin Deficiency
- Status
- RECRUITING
- Phase
- PHASE1
Clinical Trials Related to Alpha 1-Antitrypsin Deficiency
Related studies linked through entity extraction aliases.
Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE1
PiMZ Longitudinal Cohort (PiMZ Logic)
- Status
- RECRUITING
- Phase
- N/A
A Study to Evaluate the Safety and Efficacy of BEAM-302 in Adult Patients With Alpha-1 Antitrypsin Deficiency (AATD)
- Status
- RECRUITING
- Phase
- PHASE1/PHASE2
A Study of KB408 for the Treatment of Alpha-1 Antitrypsin Deficiency
- Status
- RECRUITING
- Phase
- PHASE1
Long-term, Open-label Study of SAR447537 (INBRX-101) in Adults With Alpha-1 Antitrypsin Deficiency Emphysema
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE2
Study of SAR447537 (INBRX-101) Compared to Plasma-derived A1PI Therapy in Adults With AATD Emphysema
- Status
- COMPLETED
- Phase
- PHASE2
Baby Detect : Genomic Newborn Screening
- Status
- COMPLETED
- Phase
- N/A
A Phase 1, First-in-human Study of VX-634
- Status
- COMPLETED
- Phase
- PHASE1
Alpha-1 Antitrypsin Disease Cohort: Longitudinal Biomarker Study of Disease
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- N/A
An Extension Study of Belcesiran in Patients With Alpha-1 Antitrypsin Deficiency Associated Liver Disease (AATLD)
- Status
- WITHDRAWN
- Phase
- PHASE2
Functional and Structural Lung Imaging in Chronic Obstructive Pulmonary Disease
- Status
- UNKNOWN
- Phase
- N/A
A Study of Belcesiran in Patients With AATLD
- Status
- TERMINATED
- Phase
- PHASE2
Phase III, Efficacy and Safety of "Kamada-AAT for Inhalation"
- Status
- RECRUITING
- Phase
- PHASE3
EARCO REGISTRY. History Of Patients With Alpha-1 Antitrypsin
- Status
- UNKNOWN
- Phase
- N/A
Study of DCR-A1AT in Healthy Adult Volunteers
- Status
- COMPLETED
- Phase
- PHASE1
Evaluation of the Efficacy and Safety of VX-814 in Subjects With the PiZZ Genotype
- Status
- TERMINATED
- Phase
- PHASE2
Alpha-1 Research Registry
- Status
- RECRUITING
- Phase
- N/A
Study of Fazirsiran (TAK-999, ARO-AAT) in Patients With Alpha-1 Antitrypsin Deficiency Associated Liver Disease (AATD)
- Status
- COMPLETED
- Phase
- PHASE2
Safety, Tolerability and Pharmacodynamic Effect of Fazirsiran (TAK-999, ARO-AAT)
- Status
- COMPLETED
- Phase
- PHASE2