An Open-Label Phase 3 Study of BMN 165 for Adults With PKU Not Previously Treated w/ BMN 165
- Status
- COMPLETED
- Phase
- PHASE3
Clinical Trials Related to BioMarin Pharmaceutical
Related studies linked through entity extraction aliases.
A Pilot Study on Diurnal Variation
- Status
- TERMINATED
- Phase
- NA
A Study of the Safety, Tolerability & Efficacy of Long-term Administration of Drisapersen in US & Canadian Subjects
- Status
- TERMINATED
- Phase
- PHASE3
A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.
- Status
- TERMINATED
- Phase
- N/A
Psychological Concomitants of Morquio Syndrome (The MAP Study)
- Status
- COMPLETED
- Phase
- N/A
Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA
- Status
- TERMINATED
- Phase
- N/A
Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease
- Status
- COMPLETED
- Phase
- N/A
Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
- Status
- TERMINATED
- Phase
- PHASE2
The Effects of Sapropterin Dihydrochloride Supplementation on in Vivo Redox Status in Patients With Classical PKU
- Status
- WITHDRAWN
- Phase
- N/A
Effects of Kuvan on Melatonin Secretion
- Status
- COMPLETED
- Phase
- PHASE4
Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome
- Status
- TERMINATED
- Phase
- PHASE2
A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia
- Status
- COMPLETED
- Phase
- N/A
A Study to Evaluate Safety and Tolerability of BMN 111 Administered to Healthy Adult Volunteers
- Status
- COMPLETED
- Phase
- PHASE1
A Study to Evaluate Subcutaneously Administered rAvPAL-PEG in Patients With Phenylketonuria for 24 Weeks
- Status
- COMPLETED
- Phase
- PHASE2
Bone Mineral Density in Adults With Hyperphenylalaninemia on Kuvan Therapy
- Status
- TERMINATED
- Phase
- NA
Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)
- Status
- COMPLETED
- Phase
- PHASE2
Extension Study for Patients Who Have Participated in a BMN 701 Study
- Status
- TERMINATED
- Phase
- PHASE2
Study of Kuvan Treatment in Adults With GTPCH Deficiency
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
- Status
- COMPLETED
- Phase
- PHASE3
Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02
- Status
- COMPLETED
- Phase
- N/A