4 participants
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
- Study Type:
- INTERVENTIONAL
- Last Updated:
- 2024-11-27
- Start Date:
- 2020-10-01
- Completion:
- 2032-04-30
Conditions
- Pompe Disease
- Pompe Disease (Late-onset)
- Glycogen Storage Disease Type 2
- Glycogen Storage Disease Type II
- LOPD
- Lysosomal Storage Diseases
- Acid Maltase Deficiency
Interventions
- GENETIC
No Results Yet