Clinical Trials

Showing trials with last updates posted in 2020.

NCT02090959 | TERMINATED | PHASE3
219 participants

An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy

Study Type:
INTERVENTIONAL
Last Updated:
2020-08-11
Start Date:
2014-03-20
Completion:
2018-06-12
Conditions
  • Muscular Dystrophy, Duchenne
  • Muscular Dystrophies
  • Muscular Disorders, Atrophic
  • Muscular Diseases
  • Musculoskeletal Diseases
  • Neuromuscular Diseases
  • Nervous System Diseases
  • Genetic Diseases, X-Linked
  • Genetic Diseases, Inborn
Interventions
  • DRUG
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