Clinical Trials

Showing trials with last updates posted in 2016.

NCT00694109 | COMPLETED | PHASE3
144 participants

An Open-label Extension Study to Assess the Long-term Safety and Efficacy of ISIS 301012 (Mipomersen) in Patients With Familial Hypercholesterolemia or Severe-Hypercholesterolemia

Study Type:
INTERVENTIONAL
Last Updated:
2016-09-09
Start Date:
2008-04-30
Completion:
2014-09-30
Conditions
  • Lipid Metabolism, Inborn Errors
  • Hypercholesterolemia, Autosomal Dominant
  • Hyperlipidemias
  • Metabolic Diseases
  • Hyperlipoproteinemia Type II
  • Metabolism, Inborn Errors
  • Genetic Diseases, Inborn
  • Infant, Newborn, Diseases
  • Metabolic Disorder
  • Congenital Abnormalities
  • Hypercholesterolemia
  • Hyperlipoproteinemias
  • Dyslipidemias
  • Lipid Metabolism Disorders
Interventions
  • DRUG
NCT00607373 | COMPLETED | PHASE3
51 participants

Study to Assess the Safety and Efficacy of ISIS 301012 (Mipomersen) in Homozygous Familial Hypercholesterolemia

Study Type:
INTERVENTIONAL
Last Updated:
2016-09-09
Start Date:
2007-07-31
Completion:
2009-03-31
Conditions
  • Lipid Metabolism, Inborn Errors
  • Hypercholesterolemia, Autosomal Dominant
  • Hyperlipidemias
  • Metabolic Diseases
  • Hyperlipoproteinemia Type II
  • Metabolism, Inborn Errors
  • Genetic Diseases, Inborn
  • Infant, Newborn, Diseases
  • Metabolic Disorder
  • Congenital Abnormalities
  • Hypercholesterolemia
  • Hyperlipoproteinemias
  • Dyslipidemias
  • Lipid Metabolism Disorders
Interventions
  • DRUG
NCT00477594 | COMPLETED | PHASE2
21 participants

Open Label Extension of ISIS 301012 (Mipomersen) to Treat Familial Hypercholesterolemia

Study Type:
INTERVENTIONAL
Last Updated:
2016-09-09
Start Date:
2007-05-31
Completion:
2011-03-31
Conditions
  • Lipid Metabolism, Inborn Errors
  • Hypercholesterolemia, Autosomal Dominant
  • Hyperlipidemias
  • Metabolic Diseases
  • Hyperlipoproteinemia Type II
  • Metabolism, Inborn Errors
  • Genetic Diseases, Inborn
  • Infant, Newborn, Diseases
  • Metabolic Disorder
  • Congenital Abnormalities
  • Hypercholesterolemia
  • Hyperlipoproteinemias
  • Dyslipidemias
  • Lipid Metabolism Disorders
Interventions
  • DRUG
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