Luspatercept in Patients Affected With Rare Inherited Anemias
NCT07331818 · Status: NOT_YET_RECRUITING · Phase: PHASE2 · Type: INTERVENTIONAL · Enrollment: 45
Last updated 2026-01-12
Summary
This is a prospective multicenter phase II basket trial evaluating Luspatercept in patients affected with rare inherited anemias
Conditions
- Hereditary Red Blood Cell Disorder (Disorder)
Interventions
- DRUG
-
Reblozyl 25 mg powder for solution for injection / Reblozyl 75 mg powder for solution for injection
Sponsors & Collaborators
-
EuroBloodNet Association
lead OTHER
Principal Investigators
-
Thierry Leblanc, Phd · Assistance Publique Hôpitaux de Paris - Hôpital Robert-Debré
Study Design
- Allocation
- NA
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Min Age
- 18 Years
- Max Age
- 99 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2026-01-15
- Primary Completion
- 2028-09-30
- Completion
- 2029-09-30
Countries
- France
- Italy
Study Locations
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