Patients With Congenital Myasthenic Syndrome Will be Treated With Mesenchymal Stem Cell Exosome Solution
NCT07226726 · Status: RECRUITING · Phase: PHASE1 · Type: INTERVENTIONAL · Enrollment: 20
Last updated 2025-11-10
Summary
Patients with Congenital Myasthenic Syndrome will be treated with Mesenchymal Stem Cell Exosome solution.
Conditions
- Congenital Myasthenic Syndrome
Interventions
- BIOLOGICAL
-
AlloEx exosomes
This is an intranasal treatment of exosomes derived from mesenchymal stem cells.
Sponsors & Collaborators
-
The Foundation for Orthopaedics and Regenerative Medicine
lead OTHER
Study Design
- Allocation
- NA
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2025-01-01
- Primary Completion
- 2028-12-31
- Completion
- 2028-12-31
Countries
- United States
- Antigua and Barbuda
Study Locations
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