Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia
NCT07073014 · Status: ENROLLING_BY_INVITATION · Phase: PHASE3 · Type: INTERVENTIONAL · Enrollment: 140
Last updated 2025-07-18
Summary
The purpose of this study is to evaluate the long-term safety and efficacy of daily doses of vosoritide in participants with HCH
Conditions
Interventions
- DRUG
-
Vosoritide
Open-label administration of vosoritide using weight-band dosing
Sponsors & Collaborators
- lead INDUSTRY
Study Design
- Allocation
- NA
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2025-06-20
- Primary Completion
- 2040-12-31
- Completion
- 2040-12-31
- FDA Drug
- Yes
Countries
- United States
- Australia
- Canada
- France
- Germany
- Italy
- Japan
- Spain
- United Kingdom
Study Locations
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