CS-206 in Patients With Sickle Cell Disease
NCT06565026 · Status: RECRUITING · Phase: EARLY_PHASE1 · Type: INTERVENTIONAL · Enrollment: 5
Last updated 2026-02-10
Summary
The goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 injection in treating sickle cell disease.
Conditions
Interventions
- GENETIC
-
CS-206
Autologous CD34+ hematopoietic stem cell suspension modified by in vitro base editing technique
Sponsors & Collaborators
-
First Affiliated Hospital of Guangxi Medical University
collaborator OTHER -
CorrectSequence Therapeutics Co., Ltd
lead INDUSTRY
Principal Investigators
-
Yongrong Lai, M.D. · First Affiliated Hospital of Guangxi Medical University
Study Design
- Allocation
- NA
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Min Age
- 12 Years
- Max Age
- 35 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2024-09-02
- Primary Completion
- 2026-12-31
- Completion
- 2027-06-30
Countries
- China
Study Locations
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