Donidalorsen Expanded Access Program for Patients With Hereditary Angioedema
NCT06415448 · Status: AVAILABLE · Type: EXPANDED_ACCESS
Last updated 2025-07-11
Summary
The purpose of the Expanded Access Program is to provide pre-approval access of donidalorsen to eligible patients with Hereditary Angioedema (HAE) who complete the ISIS 721744-CS3 clinical trial.
Conditions
Interventions
- DRUG
-
Donidalorsen
Donidalorsen administered once monthly or every other month by subcutaneous (SC) injections in the abdomen, thigh, or upper arm.
Sponsors & Collaborators
-
Ionis Pharmaceuticals, Inc.
lead INDUSTRY
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
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