Danon Disease Natural History Study
NCT06214507 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 60
Last updated 2026-05-05
Summary
The goal of this international observational study is to learn about the natural history of Danon disease in male patients (≥8 years of age) and female patients (8 to 50 years of age).
Conditions
- Danon Disease
Interventions
- OTHER
-
No intervention
No intervention
Sponsors & Collaborators
-
Rocket Pharmaceuticals Inc.
lead INDUSTRY
Eligibility
- Min Age
- 8 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2023-12-20
- Primary Completion
- 2029-12-31
- Completion
- 2030-03-31
Countries
- United States
- Germany
- Israel
- Italy
- Spain
- United Kingdom
Study Locations
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