Trial Outcomes & Findings for Tolerability and Immunogenicity of a Single 40-ug Dose of rBV A/B for the Production of BabyBIG® (NCT NCT06112834)

NCT ID: NCT06112834

Last Updated: 2026-07-30

Results Overview

The primary immunogenicity endpoint is the proportion of participants achieving a three or four times or greater increase in NAC by Week 4 compared with Week 0. A positive response will be defined as achieving this level of increase in at least 50% of the participants for botulinum toxin type A and type B.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

25 participants

Primary outcome timeframe

Week 0 to Week 4

Results posted on

2026-07-30

Participant Flow

A total of 25 participants were enrolled during the recruiting period from 09 July 2024 to 17 October 2024.

All enrolled participants participated in the study.

Participant milestones

Participant milestones
Measure
0.5 mL rBV A/B
A single 0.5-mL intramuscular injection of 40 μg of rBV A/B was administered to each participant on Day 0 to stimulate the production of antibodies against botulinum toxin type A and type B.
Overall Study
STARTED
25
Overall Study
Screening
25
Overall Study
Participants received rBV A/B injection
25
Overall Study
Participants included in the plasma-donating population
22
Overall Study
Participants completed follow up
25
Overall Study
COMPLETED
25
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Tolerability and Immunogenicity of a Single 40-ug Dose of rBV A/B for the Production of BabyBIG®

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
0.5 mL rBV A/B
n=25 Participants
A single 0.5-mL intramuscular injection of 40 μg of rBV A/B was administered to each participant on Day 0 to stimulate the production of antibodies against botulinum toxin type A and type B.
Age, Categorical
<=18 years
0 Participants
n=20 Participants
Age, Categorical
Between 18 and 65 years
23 Participants
n=20 Participants
Age, Categorical
>=65 years
2 Participants
n=20 Participants
Age, Continuous
48.0 years
n=20 Participants
Sex: Female, Male
Female
15 Participants
n=20 Participants
Sex: Female, Male
Male
10 Participants
n=20 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=20 Participants
Race (NIH/OMB)
Asian
5 Participants
n=20 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=20 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=20 Participants
Race (NIH/OMB)
White
19 Participants
n=20 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=20 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=20 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=20 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
25 Participants
n=20 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=20 Participants
Region of Enrollment
United States
25 Participants
n=20 Participants
Previous BabyBIG Plasma Donor
24 Participants
n=20 Participants

PRIMARY outcome

Timeframe: Week 0 to Week 4

Population: Immunogenicity Population: All participants who received rBV A/B, had a baseline NAC, and had at least one post-vaccination immunogenicity assessment up to and including four weeks after administration of rBV A/B

The primary immunogenicity endpoint is the proportion of participants achieving a three or four times or greater increase in NAC by Week 4 compared with Week 0. A positive response will be defined as achieving this level of increase in at least 50% of the participants for botulinum toxin type A and type B.

Outcome measures

Outcome measures
Measure
0.5 mL rBV A/B
n=25 Participants
A single 0.5-mL intramuscular injection of 40 μg of rBV A/B was administered to each participant on Day 0 to stimulate the production of antibodies against botulinum toxin type A and type B.
Proportion of Subjects Achieving Equal to or Greater Than 4-Fold Increase in Neutralizing Antibody Concentration (NAC)
Proportion of participants with a ≥3 × increase in Type A NAC
0.84 proportion of participants
Interval 0.639 to 0.955
Proportion of Subjects Achieving Equal to or Greater Than 4-Fold Increase in Neutralizing Antibody Concentration (NAC)
Proportion of participants with a ≥4 × increase in type A NAC
0.84 proportion of participants
Interval 0.639 to 0.955
Proportion of Subjects Achieving Equal to or Greater Than 4-Fold Increase in Neutralizing Antibody Concentration (NAC)
Proportion of participants with a ≥4 × increase in Type B NAC
0.76 proportion of participants
Interval 0.549 to 0.906
Proportion of Subjects Achieving Equal to or Greater Than 4-Fold Increase in Neutralizing Antibody Concentration (NAC)
Proportion of participants with a ≥3 × increase in Type B NAC
0.84 proportion of participants
Interval 0.639 to 0.955

SECONDARY outcome

Timeframe: Week 0 to Week 12

Population: Immunogenicity Population: All participants who received rBV A/B, had a baseline NAC, and had at least one post-vaccination immunogenicity assessment up to and including four weeks after administration of rBV A/B

The proportion of participants achieving two times increase in the area under the plasma concentration-time curve between Week 0 and Week 12 in NAC in comparison to a straight-line extension of the Week 0 NAC to Week 12. A positive response will be defined as achieving this level of increase in at least 50% of participants for botulinum toxin type A and type B.

Outcome measures

Outcome measures
Measure
0.5 mL rBV A/B
n=25 Participants
A single 0.5-mL intramuscular injection of 40 μg of rBV A/B was administered to each participant on Day 0 to stimulate the production of antibodies against botulinum toxin type A and type B.
Proportion of Subjects Achieving 2-Fold Increase in Area Under the Plasma Concentration-Time Curve in Neutralizing Antibody Concentration (NAC)
two times or greater increase in type A NAC compared with Week 0
0.92 proportion of participants
Interval 0.74 to 0.99
Proportion of Subjects Achieving 2-Fold Increase in Area Under the Plasma Concentration-Time Curve in Neutralizing Antibody Concentration (NAC)
two times or greater increase in type B NAC compared with Week 0
0.92 proportion of participants
Interval 0.74 to 0.99

OTHER_PRE_SPECIFIED outcome

Timeframe: Week 0 to Week 12

Population: Plasma-Donating Population: all participants who received rBV A/B and donated at least one plasma unit. All participants (n=22) in the plasma-donating population had positive anti-A and anti-B titers.

The volume of source plasma containing neutralizing antibodies against botulinum toxin type A and type B collected by plasmapheresis for use in BabyBIG manufacture.

Outcome measures

Outcome measures
Measure
0.5 mL rBV A/B
n=22 Participants
A single 0.5-mL intramuscular injection of 40 μg of rBV A/B was administered to each participant on Day 0 to stimulate the production of antibodies against botulinum toxin type A and type B.
Volume of Plasma Collected With Anti-Botulinum Toxin Type A and Anti-Botulinum Toxin Type B Antibody Titers
Total volume of plasma from all donating participants
356,436 mL
Volume of Plasma Collected With Anti-Botulinum Toxin Type A and Anti-Botulinum Toxin Type B Antibody Titers
Total volume of plasma from all donating participants with a positive titer (mg[%])
356,436 mL
Volume of Plasma Collected With Anti-Botulinum Toxin Type A and Anti-Botulinum Toxin Type B Antibody Titers
Total volume of plasma from donating participants with positive anti-A titer
356,436 mL
Volume of Plasma Collected With Anti-Botulinum Toxin Type A and Anti-Botulinum Toxin Type B Antibody Titers
Total volume of plasma from donating participants with positive anti-B titer
356,436 mL

Adverse Events

0.5 mL rBV A/B

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Jessica M. Khouri, M.D., Senior Medical Officer

California Department of Public Health

Phone: 510-231-7600

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place