Trial Outcomes & Findings for GV1001 Subcutaneous(SC) for the Treatment of Progressive Supranuclear Palsy (PSP) (NCT NCT05819658)

NCT ID: NCT05819658

Last Updated: 2026-02-10

Results Overview

Change from the baseline in the total score of PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 100 with a higher score indicating severely impaired cognitive function.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

78 participants

Primary outcome timeframe

24 weeks(6 months)

Results posted on

2026-02-10

Participant Flow

Participant milestones

Participant milestones
Measure
Placebo
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 0.56 mg
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Overall Study
STARTED
25
25
28
Overall Study
COMPLETED
22
20
25
Overall Study
NOT COMPLETED
3
5
3

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Race and Ethnicity were not collected from any participant.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=25 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 0.56 mg
n=25 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=28 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Total
n=78 Participants
Total of all reporting groups
Sex: Female, Male
Female
11 Participants
n=25 Participants
9 Participants
n=25 Participants
6 Participants
n=28 Participants
26 Participants
n=78 Participants
Sex: Female, Male
Male
14 Participants
n=25 Participants
16 Participants
n=25 Participants
22 Participants
n=28 Participants
52 Participants
n=78 Participants
Race and Ethnicity Not Collected
0 Participants
Race and Ethnicity were not collected from any participant.
Region of Enrollment
South Korea
25 Participants
n=25 Participants
25 Participants
n=25 Participants
28 Participants
n=28 Participants
78 Participants
n=78 Participants
PSP type
PSP-Richardson type
18 Participants
n=25 Participants
16 Participants
n=25 Participants
21 Participants
n=28 Participants
55 Participants
n=78 Participants
PSP type
PSP Parkinsonian type
7 Participants
n=25 Participants
9 Participants
n=25 Participants
7 Participants
n=28 Participants
23 Participants
n=78 Participants
Age, Categorical
<=18 years
0 Participants
n=25 Participants
0 Participants
n=25 Participants
0 Participants
n=28 Participants
0 Participants
n=78 Participants
Age, Categorical
Between 18 and 65 years
6 Participants
n=25 Participants
7 Participants
n=25 Participants
3 Participants
n=28 Participants
16 Participants
n=78 Participants
Age, Categorical
>=65 years
19 Participants
n=25 Participants
18 Participants
n=25 Participants
25 Participants
n=28 Participants
62 Participants
n=78 Participants

PRIMARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the total score of PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 100 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Total Score of PSP-rating Scale
2.14 scores on a scale
Standard Deviation 1.78
6.46 scores on a scale
Standard Deviation 1.64
4.10 scores on a scale
Standard Deviation 1.69

SECONDARY outcome

Timeframe: 12 Weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the total score of PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 100 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Total Score of PSP-rating Scale
-0.47 scores on a scale
Standard Deviation 1.65
2.75 scores on a scale
Standard Deviation 1.55
1.42 scores on a scale
Standard Deviation 1.60

SECONDARY outcome

Timeframe: 12 weeks (3 Months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the Montreal Cognitive Assessment - Korea (MoCAK) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 30 with a higher score indicating greater cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Montreal Cognitive Assessment - Korea (MoCAK)
0.93 scores on a scale
Standard Deviation 0.64
0.26 scores on a scale
Standard Deviation 0.60
0.25 scores on a scale
Standard Deviation 0.61

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the Montreal Cognitive Assessment - Korea (MoCAK) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 30 with a higher score indicating greater cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Montreal Cognitive Assessment - Korea (MoCAK)
0.35 scores on a scale
Standard Deviation 0.78
-1.46 scores on a scale
Standard Deviation 0.71
0.29 scores on a scale
Standard Deviation 0.73

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the Korean Frontal Assessment Battery (K-FAB) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 18 with a higher score indicating greater cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Korean Frontal Assessment Battery (K-FAB)
-1.06 scores on a scale
Standard Deviation 0.53
-1.42 scores on a scale
Standard Deviation 0.49
-0.29 scores on a scale
Standard Deviation 0.51

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the Korean Frontal Assessment Battery (K-FAB) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 18 with a higher score indicating greater cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Korean Frontal Assessment Battery (K-FAB)
-0.89 scores on a scale
Standard Deviation 0.59
-1.42 scores on a scale
Standard Deviation 0.54
-0.20 scores on a scale
Standard Deviation 0.55

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the England \& Schwab Activity of Daily Living (ES ADL) scale after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 (complete dependence) to 100% (complete independence) based on the level of independence.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the England & Schwab Activity of Daily Living (ES ADL) Scale
-2.70 scores on a scale
Standard Deviation 3.02
-7.12 scores on a scale
Standard Deviation 2.85
-2.18 scores on a scale
Standard Deviation 2.92

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the England \& Schwab Activity of Daily Living (ES ADL) scale after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 (complete dependence) to 100% (complete independence) based on the level of independence.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the England & Schwab Activity of Daily Living (ES ADL) Scale
-8.35 scores on a scale
Standard Deviation 3.23
-17.12 scores on a scale
Standard Deviation 2.99
-9.45 scores on a scale
Standard Deviation 3.05

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the score of \[History\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 24 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (History)
-0.17 scores on a scale
Standard Deviation 0.59
0.41 scores on a scale
Standard Deviation 0.55
-0.26 scores on a scale
Standard Deviation 0.56

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the score of \[History\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 24 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (History)
0.90 scores on a scale
Standard Deviation 0.70
1.36 scores on a scale
Standard Deviation 0.64
0.42 scores on a scale
Standard Deviation 0.66

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the score of \[Mentation\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 16 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Mentation)
-0.01 scores on a scale
Standard Deviation 0.41
0.23 scores on a scale
Standard Deviation 0.39
0.31 scores on a scale
Standard Deviation 0.41

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the score of \[Mentation\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 16 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Mentation)
-0.07 scores on a scale
Standard Deviation 0.43
0.66 scores on a scale
Standard Deviation 0.40
0.26 scores on a scale
Standard Deviation 0.41

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the score of \[Bulbar\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 8 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Bulbar)
0.11 scores on a scale
Standard Deviation 0.25
-0.08 scores on a scale
Standard Deviation 0.24
0.35 scores on a scale
Standard Deviation 0.24

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the score of \[Bulbar\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 8 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Bulbar)
0.04 scores on a scale
Standard Deviation 0.28
0.68 scores on a scale
Standard Deviation 0.26
0.49 scores on a scale
Standard Deviation 0.26

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the score of \[Ocular Motor\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 16 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Ocular Motor)
0.08 scores on a scale
Standard Deviation 0.49
0.86 scores on a scale
Standard Deviation 0.46
-0.05 scores on a scale
Standard Deviation 0.48

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the score of \[Ocular Motor\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 16 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Ocular Motor)
0.25 scores on a scale
Standard Deviation 0.46
1.30 scores on a scale
Standard Deviation 0.43
1.36 scores on a scale
Standard Deviation 0.44

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the score of \[Limb Motor\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 16 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Limb Motor)
-0.26 scores on a scale
Standard Deviation 0.38
0.02 scores on a scale
Standard Deviation 0.36
0.27 scores on a scale
Standard Deviation 0.36

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the score of \[Limb Motor\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 16 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Limb Motor)
-0.07 scores on a scale
Standard Deviation 0.55
0.51 scores on a scale
Standard Deviation 0.50
0.45 scores on a scale
Standard Deviation 0.52

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the score of \[Midline/Gait\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 12 weeks (3 months) of investigational product administration. The possible total scores range from 0 to 20 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Midline/Gait)
-0.08 scores on a scale
Standard Deviation 0.49
1.19 scores on a scale
Standard Deviation 0.46
0.26 scores on a scale
Standard Deviation 0.47

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the score of \[Midline/Gait\] domain of the PSP-rating scale(Progressive Supranuclear Palsy Rating Scale) after 24 weeks (6 months) of investigational product administration. The possible total scores range from 0 to 20 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Domain of the PSP-rating Scale (Midline/Gait)
1.28 scores on a scale
Standard Deviation 0.59
1.79 scores on a scale
Standard Deviation 0.54
0.58 scores on a scale
Standard Deviation 0.56

SECONDARY outcome

Timeframe: 12 weeks(3 months)

Population: Participants who completed 12 weeks (3 months) were included.

Change from the baseline in the score of each item \[Item 12\_Dysarthria\] of the PSP-rating scale after 12 weeks (3 months) of investigational product administration. Only the analysis result for Item no.12 out of a total of 28 items is described. The possible total scores range from 0 to 4 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=22 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=26 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Item of the PSP-rating Scale(Item 12_Dysarthria)
0.13 scores on a scale
Standard Deviation 0.15
0.06 scores on a scale
Standard Deviation 0.14
0.21 scores on a scale
Standard Deviation 0.15

SECONDARY outcome

Timeframe: 24 weeks(6 months)

Population: Participants who completed 24 weeks (6 months) were included.

Change from the baseline in the score of each item \[Item 12\_Dysarthria\] of the PSP-rating scale after 24 weeks (6 months) of investigational product administration. Only the analysis result for Item no.12 out of a total of 28 items is described. The possible total scores range from 0 to 4 with a higher score indicating severely impaired cognitive function.

Outcome measures

Outcome measures
Measure
GV1001 0.56 mg
n=20 Participants
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=25 Participants
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Placebo
n=22 Participants
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Change From the Baseline in the Score of Each Item of the PSP-rating Scale(Item 12_Dysarthria)
0.01 scores on a scale
Standard Deviation 0.15
0.44 scores on a scale
Standard Deviation 0.14
0.44 scores on a scale
Standard Deviation 0.14

Adverse Events

Placebo

Serious events: 3 serious events
Other events: 15 other events
Deaths: 0 deaths

GV1001 0.56 mg

Serious events: 2 serious events
Other events: 12 other events
Deaths: 0 deaths

GV1001 1.12 mg

Serious events: 5 serious events
Other events: 9 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Placebo
n=24 participants at risk
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 0.56 mg
n=24 participants at risk
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=28 participants at risk
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Infections and infestations
Pneumonia aspiration
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Infections and infestations
Infective spondylitis
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Infections and infestations
Tuberculous pleurisy
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Injury, poisoning and procedural complications
Clavicle fracture
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Injury, poisoning and procedural complications
Joint dislocation
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Injury, poisoning and procedural complications
Rib fracture
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Injury, poisoning and procedural complications
Spinal fracture
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Cardiac disorders
Acute myocardial infarction
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Gastrointestinal disorders
Gastric ulcer
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Colon cancer
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Psychiatric disorders
Suicide attempt
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)

Other adverse events

Other adverse events
Measure
Placebo
n=24 participants at risk
Placebo SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 0.56 mg
n=24 participants at risk
GV1001 0.56 mg SC injection will be administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
GV1001 1.12 mg
n=28 participants at risk
GV1001 1.12 mg SC injection administered once weekly for 4 weeks then every 2 weeks through Week 24 for double blind phase.
Injury, poisoning and procedural complications
Skin laceration
8.3%
2/24 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
8.3%
2/24 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Injury, poisoning and procedural complications
Skin abrasion
8.3%
2/24 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
General disorders
Injection site erythema
8.3%
2/24 • Number of events 11 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
4.2%
1/24 • Number of events 4 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
10.7%
3/28 • Number of events 9 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
General disorders
Chest pain
12.5%
3/24 • Number of events 3 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
General disorders
Pyrexia
8.3%
2/24 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Gastrointestinal disorders
Constipation
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
12.5%
3/24 • Number of events 3 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
7.1%
2/28 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Gastrointestinal disorders
Gastric ulcer
8.3%
2/24 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Gastrointestinal disorders
Toothache
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
7.1%
2/28 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Infections and infestations
Nasopharyngitis
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
8.3%
2/24 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Psychiatric disorders
Depression
0.00%
0/24 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
8.3%
2/24 • Number of events 2 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
0.00%
0/28 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
Nervous system disorders
Dizziness
4.2%
1/24 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
8.3%
2/24 • Number of events 3 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)
3.6%
1/28 • Number of events 1 • From enrollment until end of follow-up, up to 28 weeks
Participants who were not treated were excluded.(0.56mg/day group: 1. Placebo group: 1)

Additional Information

Hyuck Lee, Clinical Research Manager

GemVax & Kael

Phone: +82 070 8633 6925

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place