Trial Outcomes & Findings for Bioequivalence Binimetinib 3 x 15 mg and 45 mg Formulations (NCT NCT05810740)

NCT ID: NCT05810740

Last Updated: 2024-09-19

Results Overview

The AUC is a measure of systemic drug exposure, which is obtained by collecting a series of blood samples and measuring the concentrations of drug in each sample. AUClast is defined as area under the concentration from zero to the last quantifiable plasma concentration.

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

37 participants

Primary outcome timeframe

Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Results posted on

2024-09-19

Participant Flow

Participant milestones

Participant milestones
Measure
Binimetinib 15 mg Then Binimetinib 45 mg
Participants first received a single dose of 3 tablets of Binimetinib 15 mg orally in fasted conditions in the morning on day 1 of a 5-day period. After a washout period of 7 days, they then received a single dose of 1 tablet of Binimetinib 45 mg orally in fasted conditions in the morning for five days on day 1 of a second 5-day period.
Binimetinib 45 mg Then Binimetinib 15 mg
Participants first received a single dose of 1 tablet of Binimetinib 45 mg orally in fasted conditions in the morning on day 1 of a five-day period. After a washout period of 7 days, they then received a single dose of 3 tablets of Binimetinib 15 mg orally in fasted conditions in the morning on day 1 of a second five-day period.
Treatment Period 1 (5 Days)
STARTED
19
18
Treatment Period 1 (5 Days)
COMPLETED
19
18
Treatment Period 1 (5 Days)
NOT COMPLETED
0
0
Washout (7 Days)
STARTED
19
18
Washout (7 Days)
COMPLETED
19
18
Washout (7 Days)
NOT COMPLETED
0
0
Treatment Period 2 (5 Days)
STARTED
19
18
Treatment Period 2 (5 Days)
COMPLETED
19
18
Treatment Period 2 (5 Days)
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Bioequivalence Binimetinib 3 x 15 mg and 45 mg Formulations

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Binimetinib 15 mg Then Binimetinib 45 mg
n=19 Participants
Participants first received a single dose of 3 tablets of Binimetinib 15 mg orally in fasted conditions in the morning on day 1 of a 5-day period. After a washout period of 7 days, they then received a single dose of 1 tablet of Binimetinib 45 mg orally in fasted conditions in the morning for five days on day 1 of a second 5-day period.
Binimetinib 45 mg Then Binimetinib 15 mg
n=18 Participants
Participants first received a single dose of 1 tablet of Binimetinib 45 mg orally in fasted conditions in the morning on day 1 of a five-day period. After a washout period of 7 days, they then received a single dose of 3 tablets of Binimetinib 15 mg orally in fasted conditions in the morning on day 1 of a second five-day period.
Total
n=37 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
18 Participants
n=99 Participants
18 Participants
n=107 Participants
36 Participants
n=206 Participants
Age, Categorical
>=65 years
1 Participants
n=99 Participants
0 Participants
n=107 Participants
1 Participants
n=206 Participants
Age, Continuous
40.7 years
STANDARD_DEVIATION 14.05 • n=99 Participants
43.9 years
STANDARD_DEVIATION 13.35 • n=107 Participants
42.3 years
STANDARD_DEVIATION 13.62 • n=206 Participants
Sex: Female, Male
Female
3 Participants
n=99 Participants
1 Participants
n=107 Participants
4 Participants
n=206 Participants
Sex: Female, Male
Male
16 Participants
n=99 Participants
17 Participants
n=107 Participants
33 Participants
n=206 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
19 Participants
n=99 Participants
18 Participants
n=107 Participants
37 Participants
n=206 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Region of Enrollment
France
19 participants
n=99 Participants
18 participants
n=107 Participants
37 participants
n=206 Participants
Alcohol history
Never
9 Participants
n=99 Participants
1 Participants
n=107 Participants
10 Participants
n=206 Participants
Alcohol history
Current
10 Participants
n=99 Participants
17 Participants
n=107 Participants
27 Participants
n=206 Participants
Smoking history
Never
11 Participants
n=99 Participants
12 Participants
n=107 Participants
23 Participants
n=206 Participants
Smoking history
Former
8 Participants
n=99 Participants
6 Participants
n=107 Participants
14 Participants
n=206 Participants

PRIMARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The AUC is a measure of systemic drug exposure, which is obtained by collecting a series of blood samples and measuring the concentrations of drug in each sample. AUClast is defined as area under the concentration from zero to the last quantifiable plasma concentration.

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Area Under the Plasma Concentration-time Curve (AUC) From Time of Administration to Last Observed Plasma Concentration (AUClast) for Binimetinib
1786 h*ng/mL
Geometric Coefficient of Variation 23.22
1723 h*ng/mL
Geometric Coefficient of Variation 24.13

PRIMARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The AUC is a measure of systemic drug exposure, which is obtained by collecting a series of blood samples and measuring the concentrations of drug in each sample. AUCinf is defined as Area under the plasma concentration-time curve from time of administration to infinity

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
AUC From Time of Administration to Infinity (AUCinf) for Binimetinib
1834 h*ng/mL
Geometric Coefficient of Variation 23.09
1784 h*ng/mL
Geometric Coefficient of Variation 23.85

PRIMARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Cmax refers to the highest measured drug concentration which is obtained by collecting a series of blood samples and measuring the concentrations of drug in each sample. Cmax,norm is defined as Cmax divided by dose (mg) per kg body weight.

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Maximum Observed Plasma Concentration (Cmax) for Binimetinib
388.0 ng/mL
Geometric Coefficient of Variation 46.3
362.2 ng/mL
Geometric Coefficient of Variation 41.1

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Tmax refers to the time after dosing when a drug attains its highest measurable concentration (Cmax). It is obtained by collecting a series of blood samples at various times after dosing, and measuring them for drug content.

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Time to Reach Cmax (Tmax) for Binimetinib
1.0000 h
Interval 0.5 to 3.0
0.7500 h
Interval 0.5 to 2.0

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The apparent terminal elimination half-life (t½) is defined as the time necessary for the concentration of a drug to decrease by one-half in the terminal phase

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Terminal Half-life (t1/2) for Binimetinib
13.002 h
Geometric Coefficient of Variation 26.194
13.901 h
Geometric Coefficient of Variation 24.696

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The first Order Terminal Elimination Rate Constant (λz) of Binimetinib corresponds to the rate at which a drug is removed from the human system

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
First Order Terminal Elimination Rate Constant (λz) of Binimetinib
0.05331 /h
Geometric Coefficient of Variation 26.19381
0.04986 /h
Geometric Coefficient of Variation 24.69575

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The residual area under the curve is expressed as a percentage of the total AUC extrapolated from tz to ∞, based on the area under the concentration-time curve.

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Residual Area (AUC_%Extrap_obs) for Binimetinib
2.2836 % of the total AUC
Geometric Coefficient of Variation 53.7862
2.8499 % of the total AUC
Geometric Coefficient of Variation 64.4826

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Mean residence time (MRT) is defined as the average time for binimetinib to reside in the body

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Mean Residence Time (MRT) for Binimetinib
11.67 h
Geometric Coefficient of Variation 22.66
12.588 h
Geometric Coefficient of Variation 27.196

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The AUC is a measure of systemic drug exposure, which is obtained by collecting a series of blood samples and measuring the concentrations of drug in each sample. AUClast is defined as area under the concentration from zero to the last quantifiable plasma concentration of AR00426032, a metabolite of binimetinib

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Area Under the Plasma Concentration-time Curve (AUC) From Time of Administration to Last Observed Plasma Concentration (AUClast) for AR00426032
223.9 h*ng/mL
Geometric Coefficient of Variation 29.4
213.5 h*ng/mL
Geometric Coefficient of Variation 32.0

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The AUC is a measure of systemic drug exposure, which is obtained by collecting a series of blood samples and measuring the concentrations of drug in each sample. AUCinf is defined as Area under the plasma concentration-time curve from time of administration to infinity of AR00426032, a metabolite of binimetinib

Outcome measures

Outcome measures
Measure
Reference Formulation
n=16 Participants
Binimetinib 3x15 mg
Test Formulation
n=18 Participants
Binimetinib 1x45 mg
AUC From Time of Administration to Infinity (AUCinf) for AR00426032
296.8 h*ng/mL
Geometric Coefficient of Variation 18.7
287.5 h*ng/mL
Geometric Coefficient of Variation 23.3

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Cmax is referred as the maximum observed concentration of AR00426032 in blood plasma determined by bioanalysis

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Maximum Observed Plasma Concentration (Cmax) for AR00426032
41.62 ng/mL
Geometric Coefficient of Variation 41.19
37.88 ng/mL
Geometric Coefficient of Variation 44.25

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The timepoint at which the maximum concentration of AR00426032 is determined by bioanalysis in the blood plasma

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=36 Participants
Binimetinib 1x45 mg
Time to Reach Cmax (Tmax) for AR00426032
1.1250 h
Interval 0.75 to 5.0
1.000 h
Interval 0.75 to 3.0

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The apparent terminal elimination half-life (t½) is defined as the time necessary for the concentration of a drug to decrease by one-half in the terminal phase

Outcome measures

Outcome measures
Measure
Reference Formulation
n=16 Participants
Binimetinib 3x15 mg
Test Formulation
n=18 Participants
Binimetinib 1x45 mg
Terminal Half-life (t1/2) for AR00426032
13.924 h
Geometric Coefficient of Variation 24.955
13.843 h
Geometric Coefficient of Variation 19.281

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The first Order Terminal Elimination Rate Constant (λz) of AR00426032 corresponds to the rate at which a drug is removed from the human system

Outcome measures

Outcome measures
Measure
Reference Formulation
n=16 Participants
Binimetinib 3x15 mg
Test Formulation
n=18 Participants
Binimetinib 1x45 mg
First Order Terminal Elimination Rate Constant (λz) of AR00426032
0.04978 /h
Geometric Coefficient of Variation 24.95496
0.05007 /h
Geometric Coefficient of Variation 19.28093

SECONDARY outcome

Timeframe: Pre-dose = 0h and at 0.5, 0.75, 1, 1.25, 1.5, 2, 3, 4, 5, 6, 8, 10, 12, 24, 36, 48, and 72 hours post dose

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Mean residence time (MRT) is defined as the average time for AR00426032 to reside in the body

Outcome measures

Outcome measures
Measure
Reference Formulation
n=16 Participants
Binimetinib 3x15 mg
Test Formulation
n=18 Participants
Binimetinib 1x45 mg
Mean Residence Time (MRT) for AR00426032
14.900 h
Geometric Coefficient of Variation 23.150
14.952 h
Geometric Coefficient of Variation 22.934

SECONDARY outcome

Timeframe: Blood samples for hematology parameters were taken at screening, on Day -1 of each period, at H24 and H48 post-dose of each period, and at end of study (EOS)

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Clinically significant shift from baseline in blood hematology parameters (Erythrocytes (red blood cells, RBC), hematocrit, hemoglobin, platelets; leukocyte count with differential: basophils, eosinophils, lymphocytes, monocytes, neutrophils/absolute neutrophil count; RBC indices: mean corpuscular hemoglobin, mean corpuscular volume, reticulocytes/erythrocytes.)

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Changes From Baseline of Blood Hematology Parameters
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Blood samples for clinical chemistry parameters were taken at screening, on Day -1 of each period, at H24 and H48 post-dose of each period, and at EOS

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Clinically significant shift from baseline in clinical chemistry parameters (alanine aminotransferase (ALT), alkaline phosphatase (ALP), aspartate aminotransferase (AST), bilirubin, gamma glutamyl transferase (GGT), indirect bilirubin, creatinine, urea, bicarbonate, calcium, chloride, magnesium, potassium, sodium, glucose, cholesterol, urate, albumin, creatine kinase (CK), lactate dehydrogenase, protein, amylase, and lipase)

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Changes From Baseline of Clinical Chemistry Parameters
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Blood samples for coagulation parameters were taken at screening, on Day -1 of each period, at H24 and H48 post-dose of each period, and at EOS

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Clinically significant shifts from baseline in coagulation parameters (activated partial thromboplastin time and prothrombin time)

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Changes From Baseline of Coagulation Parameters
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Urinalysis samples were taken at screening, on Day -1 of each period, at H24 and H48 post-dose of each period, and at EOS

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Clinically significant changes from baseline in the quantitative assessment of pH, bilirubin, erythrocytes, glucose, ketones, leukocyte esterase, nitrite, protein, and urobilinogen

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Changes From Baseline of Urinalysis Parameters
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Vital signs were measured at screening, on Day -1 of each period, at Day 1 pre-dose, H24 and H72 post-dose of each period, and at EOS

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Number of participants with at least one clinically significant vital signs abnormality. The following clinical signs were measured: supine and standing systolic and diastolic blood pressure (mmHg), pulse rate (beats/min) body temperature (°C), body weight, and BMI

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Abnormalities Values of Vital Sign Parameters
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Vital signs were measured at screening, on Day -1 of each period, at Day 1 pre-dose, H24 and H72 post-dose of each period, and at EOS

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

The number and percentage of participants with at least one orthostatic hypotension defined as standing systolic blood pressure (SBP) - supine SBP ≤ -20 mmHg or standing diastolic blood pressure (DBP) - supine DBP ≤ -10 mmHg considered clinically significant.

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Orthostatic Hypotension
0 Participants
1 Participants

SECONDARY outcome

Timeframe: ECG abnormalities were recorded in triplicate at screening, on Day -1 of each period, at Day 1 pre-dose and H24 post-dose of each period, and at EOS

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Number of participant with at least one clinically significant electrocardiogram abnormality. The following standard 12-lead ECG parameters were recorded: heart rate (beats/min), PR interval (msec), QRS duration (msec), QRS axis (deg), QT interval (msec) and Fridericia QTc interval (msec)

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Abnormalities Values in 12-lead Electrocardiograms (ECG)
0 Participants
0 Participants

SECONDARY outcome

Timeframe: A complete physical examination was performed at screening, on Day -1 of each period, at H24 post-dose of each period, and at EOS

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Number of participants with at least one clinically significant physical examination abnormality. A complete physical examination, including at minima assessments of the cardiovascular, dermatological, ear/nose/throat, eyes, gastrointestinal, general health/overall appearance, head, lymph, musculoskeletal, neck, neurological, and respiratory systems was performed

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Clinically Significant Physical Examination Abnormalities
0 Participants
0 Participants

SECONDARY outcome

Timeframe: A visual examination was performed at Screening at at EOS.

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Visual assessment was performed at screening, on Day -1 of each period, at H24 and H72 post-dose of each period, and at EOS

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Abnormal Changes From Baseline in Visual Examinations
0 Participants
0 Participants

SECONDARY outcome

Timeframe: An opthalmologic examination was performed at Screening at at EOS.

Population: The analysis population was the pharmacokinetic set that consisted of 36 healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants was excluded from the pharmacokinetic set due to treatment discontinuation before the second treatment period.

Abnormal changes from baseline in ophthalmologic examinations including best corrected visual acuity for distance testing, optical coherence tomography and/or fluorescein angiography, slit lamp examination, IOP and dilated fundoscopy with attention to retinal abnormalities

Outcome measures

Outcome measures
Measure
Reference Formulation
n=36 Participants
Binimetinib 3x15 mg
Test Formulation
n=37 Participants
Binimetinib 1x45 mg
Abnormal Changes From Baseline in Ophthalmologic Examinations
1 Participants
0 Participants

Adverse Events

Reference Formulation

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Test Formulation

Serious events: 0 serious events
Other events: 4 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Reference Formulation
n=36 participants at risk
Binimetinib 3x15 mg
Test Formulation
n=37 participants at risk
Binimetinib 1x45 mg
Infections and infestations
Covid-19
2.8%
1/36 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
2.7%
1/37 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Infections and infestations
Tooth abscess
2.8%
1/36 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
0.00%
0/37 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Infections and infestations
Viral infection
2.8%
1/36 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
0.00%
0/37 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Eye disorders
Ocular discomfort
0.00%
0/36 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
2.7%
1/37 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Eye disorders
Retinal vascular disorder
0.00%
0/36 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
2.7%
1/37 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Eye disorders
Vision blurred
2.8%
1/36 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
0.00%
0/37 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Gastrointestinal disorders
Abdominal pain
0.00%
0/36 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
2.7%
1/37 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Gastrointestinal disorders
Anal pruritus
2.8%
1/36 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
0.00%
0/37 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Gastrointestinal disorders
Frequent bowel movements
2.8%
1/36 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
0.00%
0/37 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Gastrointestinal disorders
Toothache
2.8%
1/36 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
0.00%
0/37 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
Vascular disorders
Orthostatic hypotension
0.00%
0/36 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.
2.7%
1/37 • Number of events 1 • Adverse events (AEs) were recorded from the time of consent until the end of the follow-up period (up to 30 days after Treatment period 2) and over a total period of 47 days.
AEs were summarized by worst grade according to the NCI-CTCAE V5.0 per participant. The analysis population was the safety set that consisted of the healthy participants who had taken one dose of study treatment in the two periods. One participant of the 37 randomised participants discontinued treatment before the second treatment period and therefore did not receive the reference formulation binimetinib 15 mg.

Additional Information

Ana Catarina Pinto, Responsible Medical Officer

Pierre Fabre Médicament

Phone: 5 3450 6059

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place