Trial Outcomes & Findings for Effects of Sacrosidase and Placebo in Subjects With Fructan Intolerance (NCT NCT05703009)

NCT ID: NCT05703009

Last Updated: 2026-06-30

Results Overview

The numeric value of the Total Symptom Score (TSS) is derived from the Daily Symptom Questionnaire (DSQ). The DSQ consisted of rating the frequency in the last 24 hours and the severity of 7 symptoms, abdominal bloating, abdominal pain, abdominal cramps, abdominal gas/flatulence, constipation, nausea, and diarrhea. The daily symptom score is calculated by summing the frequency and severity scores for each symptom with a minimum daily score of 0 and a maximum daily score of 98. The TSS is calculated by averaging the combined daily symptom scores during a 7-day period for baseline and 1-week post-intervention during each treatment period and ranges from 0-98, with higher values representing a worse outcome.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

25 participants

Primary outcome timeframe

Baseline and 1 week

Results posted on

2026-06-30

Participant Flow

Participant milestones

Participant milestones
Measure
Sacrosidase, 2 ,L (17,000 IU), Then Placebo
Subjects randomized to take active treatment, sacrosidase, 2 mL (17,000 IU) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for one week.
Placebo, Then Sacrosidase 2 mL (17,000 IU)
Subjects randomized to take placebo treatment, sacrosidase placebo, 2 mL (17,000 IU) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for one week.
Treatment Period 1 (1 week)
STARTED
12
13
Treatment Period 1 (1 week)
COMPLETED
12
13
Treatment Period 1 (1 week)
NOT COMPLETED
0
0
Washout Period (1 week)
STARTED
12
13
Washout Period (1 week)
COMPLETED
12
13
Washout Period (1 week)
NOT COMPLETED
0
0
Treatment Period 2 (1 week)
STARTED
12
13
Treatment Period 2 (1 week)
COMPLETED
12
13
Treatment Period 2 (1 week)
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Effects of Sacrosidase and Placebo in Subjects With Fructan Intolerance

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Sacrosidase 2 mL (17,000 IU), Then Placebo
n=12 Participants
Subjects randomized to take active treatment, sacrosidase oral solution 17,000 IU with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for one week. After a 1-week wash-out period, subjects received placebo (matching active sacrosidase 17,000 IU) for 1 week with every meal or snack.
Placebo, Then Sacrosidase 2 mL (17,000 IU)
n=13 Participants
Subjects randomized to take placebo matching sacrosidase 17,000 IU, with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for one week. After a 1-week wash-out period, subjects received active sacrosidase oral solution 17,000 IU with every meal or snack.
Total
n=25 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=20 Participants
0 Participants
n=20 Participants
0 Participants
n=40 Participants
Age, Categorical
Between 18 and 65 years
12 Participants
n=20 Participants
13 Participants
n=20 Participants
25 Participants
n=40 Participants
Age, Categorical
>=65 years
0 Participants
n=20 Participants
0 Participants
n=20 Participants
0 Participants
n=40 Participants
Age, Continuous
36.3 years
STANDARD_DEVIATION 10.31 • n=20 Participants
35.8 years
STANDARD_DEVIATION 11.48 • n=20 Participants
36.0 years
STANDARD_DEVIATION 10.71 • n=40 Participants
Sex: Female, Male
Female
4 Participants
n=20 Participants
4 Participants
n=20 Participants
8 Participants
n=40 Participants
Sex: Female, Male
Male
8 Participants
n=20 Participants
9 Participants
n=20 Participants
17 Participants
n=40 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=20 Participants
1 Participants
n=20 Participants
1 Participants
n=40 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
12 Participants
n=20 Participants
12 Participants
n=20 Participants
24 Participants
n=40 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=20 Participants
0 Participants
n=20 Participants
0 Participants
n=40 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=20 Participants
0 Participants
n=20 Participants
0 Participants
n=40 Participants
Race (NIH/OMB)
Asian
1 Participants
n=20 Participants
2 Participants
n=20 Participants
3 Participants
n=40 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
1 Participants
n=20 Participants
0 Participants
n=20 Participants
1 Participants
n=40 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=20 Participants
0 Participants
n=20 Participants
0 Participants
n=40 Participants
Race (NIH/OMB)
White
10 Participants
n=20 Participants
11 Participants
n=20 Participants
21 Participants
n=40 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=20 Participants
0 Participants
n=20 Participants
0 Participants
n=40 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=20 Participants
0 Participants
n=20 Participants
0 Participants
n=40 Participants
Region of Enrollment
United States
12 participants
n=20 Participants
13 participants
n=20 Participants
25 participants
n=40 Participants

PRIMARY outcome

Timeframe: Baseline and 1 week

The numeric value of the Total Symptom Score (TSS) is derived from the Daily Symptom Questionnaire (DSQ). The DSQ consisted of rating the frequency in the last 24 hours and the severity of 7 symptoms, abdominal bloating, abdominal pain, abdominal cramps, abdominal gas/flatulence, constipation, nausea, and diarrhea. The daily symptom score is calculated by summing the frequency and severity scores for each symptom with a minimum daily score of 0 and a maximum daily score of 98. The TSS is calculated by averaging the combined daily symptom scores during a 7-day period for baseline and 1-week post-intervention during each treatment period and ranges from 0-98, with higher values representing a worse outcome.

Outcome measures

Outcome measures
Measure
Sacrosidase 2 mL (17,000 IU)
n=25 Participants
Subjects who received sacrosidase oral solution, 2 mL (17,000 IU) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for 1 week during Treatment Period 1 or Treatment Period 2.
Placebo
n=25 Participants
Subjects who received Placebo (matching sacrosidase oral solution) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for 1 week during Treatment Period 1 or Treatment Period 2.
Change From Baseline in Mean (SD) Total Symptom Score (TSS) at 1 Week
-4.11 units on a scale
Standard Deviation 10.736
-2.88 units on a scale
Standard Deviation 8.421

SECONDARY outcome

Timeframe: Baseline and 1 week

The Daily Symptom Questionnaire (DSQ) consisted of rating the frequency in the last 24 hours and the severity of 7 symptoms, abdominal bloating, abdominal pain, abdominal cramps, abdominal gas/flatulence, constipation, nausea, and diarrhea. The frequency score for abdominal bloating experienced is calculated by averaging the combined daily scores during a 7-day period for baseline and 1-week post-intervention during each treatment period and ranges from 0-5, with higher values representing a worse outcome.

Outcome measures

Outcome measures
Measure
Sacrosidase 2 mL (17,000 IU)
n=25 Participants
Subjects who received sacrosidase oral solution, 2 mL (17,000 IU) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for 1 week during Treatment Period 1 or Treatment Period 2.
Placebo
n=25 Participants
Subjects who received Placebo (matching sacrosidase oral solution) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for 1 week during Treatment Period 1 or Treatment Period 2.
Change From Baseline in Mean (SD) Frequency Score for Abdominal Bloating From Baseline to 1 Week
-0.50 score on a scale
Standard Deviation 1.058
-0.54 score on a scale
Standard Deviation 0.990

Adverse Events

Sacrosidase 2 mL (17,000 IU)

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Sacrosidase 2 mL (17,000 IU)
n=25 participants at risk
Subjects who received sacrosidase oral solution, 2 mL (17,000 IU) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for 1 week during Treatment Period 1 or Treatment Period 2.
Placebo
n=25 participants at risk
Subjects who received Placebo (matching sacrosidase oral solution) with every meal or snack, administered orally following dilution with 2 to 4 ounces (60 to 120 mL) of water or milk (either cold or at room temperature) for 1 week during Treatment Period 1 or Treatment Period 2.
Gastrointestinal disorders
Constipation
0.00%
0/25 • 1 week for each intervention
4.0%
1/25 • 1 week for each intervention
Gastrointestinal disorders
Worsened Gastroparesis
0.00%
0/25 • 1 week for each intervention
4.0%
1/25 • 1 week for each intervention
Reproductive system and breast disorders
Heavy Menstrual Bleeding
0.00%
0/25 • 1 week for each intervention
4.0%
1/25 • 1 week for each intervention
Infections and infestations
Food Poisoning
4.0%
1/25 • 1 week for each intervention
0.00%
0/25 • 1 week for each intervention
Skin and subcutaneous tissue disorders
Lipoma
4.0%
1/25 • 1 week for each intervention
0.00%
0/25 • 1 week for each intervention
Gastrointestinal disorders
Acid Reflux
4.0%
1/25 • 1 week for each intervention
0.00%
0/25 • 1 week for each intervention

Additional Information

Kasidy Street, Senior Clinical Project Manager & Medical Information Specialist

QOL Medical

Phone: 9198328585

Results disclosure agreements

  • Principal investigator is a sponsor employee As outlined in each Clinical Trial Agreement between Sponsor and PI.
  • Publication restrictions are in place

Restriction type: OTHER