Trial Outcomes & Findings for Procedural Discomfort Related to Number of Intradetrusor Botox Injections (NCT NCT05652036)

NCT ID: NCT05652036

Last Updated: 2025-04-13

Results Overview

Participants will assess their discomfort using the Numeric Pain Scale (NPS), a validated 11-point scale (0-10) where higher scores indicate greater pain, before and immediately after the procedure. Procedural discomfort will be evaluated by comparing the change in NPS scores from pre- to post-procedure between study groups.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

108 participants

Primary outcome timeframe

Immediately post-procedure (up to 45min after intradetrusor BTX-A injections)

Results posted on

2025-04-13

Participant Flow

Participant milestones

Participant milestones
Measure
5 mL Group
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Overall Study
STARTED
52
56
Overall Study
COMPLETED
52
56
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Procedural Discomfort Related to Number of Intradetrusor Botox Injections

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
5 mL Group
n=52 Participants
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
n=56 Participants
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Total
n=108 Participants
Total of all reporting groups
Age, Continuous
64.6 Years
STANDARD_DEVIATION 14.3 • n=99 Participants
70.6 Years
STANDARD_DEVIATION 10.3 • n=107 Participants
67.6 Years
STANDARD_DEVIATION 12.8 • n=206 Participants
Sex: Female, Male
Female
52 Participants
n=99 Participants
56 Participants
n=107 Participants
108 Participants
n=206 Participants
Sex: Female, Male
Male
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Asian
2 Participants
n=99 Participants
2 Participants
n=107 Participants
4 Participants
n=206 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Black or African American
4 Participants
n=99 Participants
8 Participants
n=107 Participants
12 Participants
n=206 Participants
Race (NIH/OMB)
White
46 Participants
n=99 Participants
45 Participants
n=107 Participants
91 Participants
n=206 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
1 Participants
n=107 Participants
1 Participants
n=206 Participants
Medical Co-Morbidities
Diabetes
9 Participants
n=99 Participants
8 Participants
n=107 Participants
17 Participants
n=206 Participants
Medical Co-Morbidities
Depression
23 Participants
n=99 Participants
18 Participants
n=107 Participants
41 Participants
n=206 Participants
Medical Co-Morbidities
Neurologic Diagnosis
15 Participants
n=99 Participants
10 Participants
n=107 Participants
25 Participants
n=206 Participants
Medical Co-Morbidities
Recurrent Urinary Tract Infection
5 Participants
n=99 Participants
12 Participants
n=107 Participants
17 Participants
n=206 Participants
Surgical History
Hysterectomy
23 Participants
n=99 Participants
35 Participants
n=107 Participants
58 Participants
n=206 Participants
Surgical History
Prolapse Repair
16 Participants
n=99 Participants
10 Participants
n=107 Participants
26 Participants
n=206 Participants
Surgical History
Incontinence Procedure
14 Participants
n=99 Participants
6 Participants
n=107 Participants
20 Participants
n=206 Participants
First Botox Injection
Yes
22 Participants
n=99 Participants
20 Participants
n=107 Participants
42 Participants
n=206 Participants
First Botox Injection
No
30 Participants
n=99 Participants
36 Participants
n=107 Participants
66 Participants
n=206 Participants

PRIMARY outcome

Timeframe: Immediately post-procedure (up to 45min after intradetrusor BTX-A injections)

Participants will assess their discomfort using the Numeric Pain Scale (NPS), a validated 11-point scale (0-10) where higher scores indicate greater pain, before and immediately after the procedure. Procedural discomfort will be evaluated by comparing the change in NPS scores from pre- to post-procedure between study groups.

Outcome measures

Outcome measures
Measure
5 mL Group
n=52 Participants
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
n=56 Participants
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Participant Discomfort Related to BTX-A Injection
3.2 score on a scale
Standard Deviation 2.3
3.6 score on a scale
Standard Deviation 2.1

SECONDARY outcome

Timeframe: Prior to BTX-A injections and 30 days post-procedure

Population: Follow-up data 30-days post-treatment was obtained from 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.

Efficacy will be evaluated using the Overactive Bladder Questionnaire Short-Form (OAB-q SF), a validated instrument designed to measure symptom bother (SB) and the impact of OAB on health-related quality of life (HRQL). This questionnaire is administered on the day of the procedure (baseline) and again 30 days post-procedure. Changes in SB and HRQL scores assess improvement in OAB symptoms following BTX-A treatment. The OAB-q SF includes 19 items divided into two subscales: a 6-item SB scale (Questions 1-6) and a 13-item HRQL scale (Questions 7-19). SB items are scored from 1 ("not at all") to 6 ("a very great deal"), yielding a total SB score range of 6 to 36, with higher scores indicating greater symptom bother. HRQL items are scored from 1 ("none of the time") to 6 ("all of the time"), with total scores ranging from 13 to 78, where higher scores reflect better quality of life. We report here the mean change in SB and HRQL scores from baseline to 30 days post-treatment.

Outcome measures

Outcome measures
Measure
5 mL Group
n=36 Participants
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
n=43 Participants
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Procedural Efficacy - Overactive Bladder Questionnaire Short-Form (OAB-q SF)
OAB-q SF (SB (mean difference))
-22.4 Units on a scale
Interval -93.0 to 73.0
-38.1 Units on a scale
Interval -100.0 to 60.0
Procedural Efficacy - Overactive Bladder Questionnaire Short-Form (OAB-q SF)
OAB-q SF (HRQL (mean difference))
14.59 Units on a scale
Interval -59.0 to 60.0
26.24 Units on a scale
Interval -30.0 to 71.0

SECONDARY outcome

Timeframe: 30 days post-procedure

Population: Thirty-day follow-up data were available for 69% (n = 36) in the 5 mL/5 injection arm and 77% (n = 43) in the 10 mL/10 injection arm.

Overall treatment satisfaction will be assessed at 30-days post-procedure via a "yes or no" response to inquiry about overall satisfaction with the procedure and results of their BTX-A treatment

Outcome measures

Outcome measures
Measure
5 mL Group
n=36 Participants
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
n=43 Participants
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Overall Treatment Satisfaction
Satisfied
33 Participants
34 Participants
Overall Treatment Satisfaction
Not Satisfied
3 Participants
9 Participants

SECONDARY outcome

Timeframe: 30 days post-procedure

Population: Thirty-day follow-up data were available for 69% (n = 36) in the 5 mL/5 injection arm and 77% (n = 43) in the 10 mL/10 injection arm.

Patients impression of clinical improvement after treatment will be assessed at 30-day post-procedure via the Clinical Global Impression - Improvement Scale (CGI-I). The CGI-I is a seven point verbal scale with higher values indicating higher impression of symptomatic improvement related to the treatment. Scale reports values as: Very much improved, Much improved, Minimally improved, No difference.

Outcome measures

Outcome measures
Measure
5 mL Group
n=36 Participants
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
n=43 Participants
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Impression of Clinical Improvement
Very much improved
9 Participants
9 Participants
Impression of Clinical Improvement
Much improved
18 Participants
16 Participants
Impression of Clinical Improvement
Minimally improved
7 Participants
15 Participants
Impression of Clinical Improvement
No difference
2 Participants
3 Participants

SECONDARY outcome

Timeframe: 30 days post-procedure

Population: Post-procedural Adverse Outcomes - Urinary retention, Urinary tract infection, Bleeding requiring evaluation, Hematuria, Bladder pain, and Emergency department evaluation. n=36 and n=43 participants were evaluated for the 5ml and 10ml arms respectively.

We will review the electronic medical record to evaluate instances of symptomatic urinary tract infection, bothersome incomplete bladder emptying requiring catheterization, and instances of bleeding requiring evaluation after the procedure.

Outcome measures

Outcome measures
Measure
5 mL Group
n=36 Participants
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
n=43 Participants
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Procedural Outcomes
Urinary retention
0 Participants
2 Participants
Procedural Outcomes
Urinary tract infection
5 Participants
2 Participants
Procedural Outcomes
Bleeding requiring evaluation
0 Participants
0 Participants
Procedural Outcomes
Hematuria
1 Participants
0 Participants
Procedural Outcomes
Bladder pain
0 Participants
1 Participants
Procedural Outcomes
Emergency department evaluation
0 Participants
2 Participants

Adverse Events

5 mL Group

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

10 mL Group

Serious events: 0 serious events
Other events: 7 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
5 mL Group
n=36 participants at risk
100 units BTX-A reconstituted in 5 mL normal saline, injected into the bladder in 5 separate injections of 1 mL. One injection will be at the trigone.
10 mL Group
n=43 participants at risk
100 units BTX-A reconstituted in 10 mL normal saline, injected into the bladder in 10 separate injections of 1 mL. One injection will be at the trigone
Renal and urinary disorders
Urinary Tract Infection
13.9%
5/36 • Number of events 5 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
4.7%
2/43 • Number of events 2 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
Renal and urinary disorders
Urinary Retention
0.00%
0/36 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
4.7%
2/43 • Number of events 2 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
Renal and urinary disorders
Bleeding Requiring Evaluation
0.00%
0/36 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
0.00%
0/43 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
Renal and urinary disorders
Hematuria
2.8%
1/36 • Number of events 1 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
0.00%
0/43 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
Renal and urinary disorders
Bladder Pain
0.00%
0/36 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
2.3%
1/43 • Number of events 1 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
Renal and urinary disorders
Emergency Department Evaluation
0.00%
0/36 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.
4.7%
2/43 • Number of events 2 • 1 month post-treatment
Thirty-day AE data were available for 69% (n = 36) of participants in the 5 mL/5 injection arm and 77% (n = 43) of participants in the 10 mL/10 injection arm.

Additional Information

Dr. Rose Khavari

Houston Methodist Hospital Department of Urology

Phone: 713-441-6455

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place