Trial Outcomes & Findings for Comparative Effectiveness Trial for Diagnosis of Necrotizing Enterocolitis (NCT NCT05573113)

NCT ID: NCT05573113

Last Updated: 2025-11-21

Results Overview

Number of days for infants to tolerate at least 120 mL/kg/day of enteral feeds

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

169 participants

Primary outcome timeframe

Within 30 days of NEC concern

Results posted on

2025-11-21

Participant Flow

Conducted between Sept 2022 - Dec 2024 at two sites: Children's Mercy Hospital (Level IV NICU) and University of Kansas Medical Center (Level III NICU).

Randomization was conducted by calendar month (odd months = AXR only; even months = AXR + BUS). Cross-over occurred in 31 AXR-only evaluations (also received BUS) and 3 AXR+BUS evaluations (only received AXR). A total of 169 infants underwent 199 imaging evaluations for NEC.

Unit of analysis: Imaging evaluation for NEC

Participant milestones

Participant milestones
Measure
Abdominal Radiographs Only (AXR)
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Overall Study
STARTED
92 114
77 85
Overall Study
Cross-Over
26 31
3 3
Overall Study
COMPLETED
92 114
77 85
Overall Study
NOT COMPLETED
0 0
0 0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Comparative Effectiveness Trial for Diagnosis of Necrotizing Enterocolitis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Abdominal Radiographs Only (AXR)
n=92 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs Plus Bowel Ultrasound (AXR + BUS)
n=77 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Total
n=169 Participants
Total of all reporting groups
Age, Continuous
31 weeks
STANDARD_DEVIATION 4.8 • n=39 Participants
31 weeks
STANDARD_DEVIATION 5.2 • n=29 Participants
31 weeks
STANDARD_DEVIATION 5 • n=60 Participants
Sex: Female, Male
Female
37 Participants
n=39 Participants
19 Participants
n=29 Participants
56 Participants
n=60 Participants
Sex: Female, Male
Male
55 Participants
n=39 Participants
58 Participants
n=29 Participants
113 Participants
n=60 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=39 Participants
0 Participants
n=29 Participants
0 Participants
n=60 Participants
Race (NIH/OMB)
Asian
3 Participants
n=39 Participants
4 Participants
n=29 Participants
7 Participants
n=60 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=39 Participants
0 Participants
n=29 Participants
0 Participants
n=60 Participants
Race (NIH/OMB)
Black or African American
21 Participants
n=39 Participants
18 Participants
n=29 Participants
39 Participants
n=60 Participants
Race (NIH/OMB)
White
46 Participants
n=39 Participants
40 Participants
n=29 Participants
86 Participants
n=60 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=39 Participants
0 Participants
n=29 Participants
0 Participants
n=60 Participants
Race (NIH/OMB)
Unknown or Not Reported
22 Participants
n=39 Participants
15 Participants
n=29 Participants
37 Participants
n=60 Participants
Birthweight
1.63 kg
STANDARD_DEVIATION 0.86 • n=39 Participants
1.66 kg
STANDARD_DEVIATION 1.10 • n=29 Participants
1.64 kg
STANDARD_DEVIATION 0.97 • n=60 Participants
Site - Level III or IV NICU
Level III
37 Participants
n=39 Participants
27 Participants
n=29 Participants
64 Participants
n=60 Participants
Site - Level III or IV NICU
Level IV
55 Participants
n=39 Participants
50 Participants
n=29 Participants
105 Participants
n=60 Participants
Multiple Gestation (%)
18 Participants
n=39 Participants
17 Participants
n=29 Participants
35 Participants
n=60 Participants
Congenital anomalies (%)
19 Participants
n=39 Participants
9 Participants
n=29 Participants
28 Participants
n=60 Participants

PRIMARY outcome

Timeframe: Within 30 days of NEC concern

Population: Extended Rule Out Group: Infants with clinical concern for NEC who were ultimately not diagnosed with NEC but required more than one AXR to confidently rule out the disease. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days for infants to tolerate at least 120 mL/kg/day of enteral feeds

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=42 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=28 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to Full Enteral Feeds: Extended Rule Out Group
10.1 days
Standard Deviation 10.9
4.9 days
Standard Deviation 4.5

PRIMARY outcome

Timeframe: Within 30 days of NEC concern

Population: Quick Rule Out Group: Infants with suspected NEC in whom the diagnosis was excluded after a single AXR. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days for infants to tolerate at least 120 mL/kg/day of enteral feeds

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=40 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=23 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to Full Enteral Feeds: Quick Rule Out Group
0.4 days
Standard Deviation 1.4
1.0 days
Standard Deviation 2.4

PRIMARY outcome

Timeframe: Within 30 days of NEC concern

Population: NEC Ruled In Group: Infants with suspected NEC who were diagnosed with NEC based on clinical, laboratory, and imaging findings. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days for infants to tolerate at least 120 mL/kg/day of enteral feeds

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=32 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=34 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to Full Enteral Feeds: NEC Ruled In
17.0 days
Standard Deviation 8.6
17.6 days
Standard Deviation 9.0

SECONDARY outcome

Timeframe: within 14 days of NEC concern

Population: Extended Rule Out Group: Infants with clinical concern for NEC who were ultimately not diagnosed with NEC but required more than one AXR to confidently rule out the disease. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days infants were kept nil per os (without enteral feeds) following concern for NEC

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=42 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=28 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to End Bowel Rest: Extended Rule Out Group
2.6 days
Standard Deviation 2.9
2.1 days
Standard Deviation 1.8

SECONDARY outcome

Timeframe: within 14 days of NEC concern

Population: Quick Rule Out Group: Infants with suspected NEC in whom the diagnosis was excluded after a single AXR. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days infants were kept nil per os (without enteral feeds) following concern for NEC

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=40 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=23 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to End Bowel Rest: Quick Rule Out Group
0.2 days
Standard Deviation 0.6
0.4 days
Standard Deviation 0.8

SECONDARY outcome

Timeframe: within 14 days of NEC concern

Population: NEC Ruled In Group: Infants with suspected NEC who were diagnosed with NEC based on clinical, laboratory, and imaging findings. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days infants were kept nil per os (without enteral feeds) following concern for NEC

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=32 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=34 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to End Bowel Rest: NEC Ruled In
8.7 days
Standard Deviation 4.0
8.7 days
Standard Deviation 3.5

SECONDARY outcome

Timeframe: within 14 days of NEC concern

Population: Extended Rule Out Group: Infants with clinical concern for NEC who were ultimately not diagnosed with NEC but required more than one AXR to confidently rule out the disease. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days infants received antibiotic therapy initiated for NEC concern

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=42 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=28 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to End Antibiotics: Extended Rule Out
1.6 days
Standard Deviation 2.3
1.5 days
Standard Deviation 2.3

SECONDARY outcome

Timeframe: within 14 days of NEC concern

Population: Quick Rule Out Group: Infants with suspected NEC in whom the diagnosis was excluded after a single AXR. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days infants received antibiotic therapy initiated for NEC concern

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=40 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=23 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to End Antibiotics: Quick Rule Out
0.1 days
Standard Deviation 0.8
0.8 days
Standard Deviation 3.1

SECONDARY outcome

Timeframe: within 14 days of NEC concern

Population: NEC Ruled In Group: Infants with suspected NEC who were diagnosed with NEC based on clinical, laboratory, and imaging findings. Infants who crossed over to a different imaging strategy were analyzed according to the arm to which they were originally randomized, following an intention-to-treat approach.

Number of days infants received antibiotic therapy initiated for NEC concern

Outcome measures

Outcome measures
Measure
Abdominal Radiographs Only (AXR)
n=32 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs only (AXR)
Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)
n=34 Participants
Infants with concern for necrotizing enterocolitis randomized to imaging with abdominal radiographs plus bowel ultrasound (AXR + BUS)
Days to End Antibiotics: NEC Rule In
8.4 days
Standard Deviation 4.0
7.5 days
Standard Deviation 3.2

Adverse Events

Abdominal Radiographs Only (AXR)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 5 deaths

Abdominal Radiographs plus Bowel Ultrasound (AXR + BUS)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 8 deaths

Cross-Over to AXR + BUS

Serious events: 0 serious events
Other events: 0 other events
Deaths: 1 deaths

Cross-Over to AXR only

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Sherwin Chan

Children's Mercy Kansas City

Phone: 816-234-3273

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place