Trial Outcomes & Findings for Ritlecitinib for Cicatricial Alopecia (NCT NCT05549934)

NCT ID: NCT05549934

Last Updated: 2026-07-15

Results Overview

Log-fold Changes in mRNA Levels of CCL5 gene expression in skin biopsies quantified by normalized Ct values obtained by quantitative real-time PCR assay, measured at baseline and week 24. The unit of the outcome is called Ct value and it represents the number of amplification cycles to reach a level of fluorescence in the experiment. The Ct value is directly associated to the level of expression of a gene

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

50 participants

Primary outcome timeframe

Baseline to Week 24

Results posted on

2026-07-15

Participant Flow

Participant milestones

Participant milestones
Measure
PF-06651600 (Ritlecitinib)
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Overall Study
STARTED
50
Overall Study
COMPLETED
30
Overall Study
NOT COMPLETED
20

Reasons for withdrawal

Reasons for withdrawal
Measure
PF-06651600 (Ritlecitinib)
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Overall Study
Adverse Event
3
Overall Study
Lack of Efficacy
3
Overall Study
Lost to Follow-up
2
Overall Study
Pregnancy
1
Overall Study
Protocol Violation
6
Overall Study
Withdrawal by Subject
3
Overall Study
Lack of Satisfaction
1
Overall Study
Not Reported
1

Baseline Characteristics

Ritlecitinib for Cicatricial Alopecia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
PF-06651600 (Ritlecitinib)
n=50 Participants
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Age, Continuous
48.72 years
STANDARD_DEVIATION 13.41 • n=20 Participants
Sex: Female, Male
Female
42 Participants
n=20 Participants
Sex: Female, Male
Male
8 Participants
n=20 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=20 Participants
Race (NIH/OMB)
Asian
1 Participants
n=20 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
1 Participants
n=20 Participants
Race (NIH/OMB)
Black or African American
21 Participants
n=20 Participants
Race (NIH/OMB)
White
27 Participants
n=20 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=20 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=20 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
5 Participants
n=20 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
45 Participants
n=20 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=20 Participants

PRIMARY outcome

Timeframe: Baseline to Week 24

Population: Data results for participants who provided data.

Log-fold Changes in mRNA Levels of CCL5 gene expression in skin biopsies quantified by normalized Ct values obtained by quantitative real-time PCR assay, measured at baseline and week 24. The unit of the outcome is called Ct value and it represents the number of amplification cycles to reach a level of fluorescence in the experiment. The Ct value is directly associated to the level of expression of a gene

Outcome measures

Outcome measures
Measure
PF-06651600 (Ritlecitinib)
n=34 Participants
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Change in Ct Values of mRNA Levels of CCL5 Gene
-1.11 amplification cycles
Standard Error 0.225

PRIMARY outcome

Timeframe: Week 48

Population: Data for participants who experienced an AE

The adverse event will be described and categorized as Treatment-emergent, Serious, abnormal in vital signals, and abnormalities in laboratory parameters.

Outcome measures

Outcome measures
Measure
PF-06651600 (Ritlecitinib)
n=43 Participants
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Number of Treatment-Emergent Adverse Events
60 events

SECONDARY outcome

Timeframe: Baseline, Week 24, and Week 48

Population: Data results for participants who provided data at timepoints

The Frontal Fibrosis Alopecia Severity Index utilizes clinical images of the entire hairline from a total score of 0-84, with higher score indicating more severity. Percent change in FFASI at Week 24 and Week 48 as compared to baseline.

Outcome measures

Outcome measures
Measure
PF-06651600 (Ritlecitinib)
n=50 Participants
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Percent Change in the Frontal Fibrosis Alopecia Severity Index (FFASI)
Week 24
-27.6 Percent change in score on a scale
Standard Error 4.6
Percent Change in the Frontal Fibrosis Alopecia Severity Index (FFASI)
Week 48
-51.3 Percent change in score on a scale
Standard Error 6.7

SECONDARY outcome

Timeframe: Baseline, Week 24 and Week 48

Population: Data results for participants who provided data at timepoints.

The Lichen Planopilaris Activity Index is a numeric composite index that aggregates symptoms and signs of pruritus, pain, burning, scalp erythema , perifollicular erythema, perifollicular scale , pull test and spreading. Symptoms and signs are measured in a 4-point scale (0-absent, 1-mild, 2-moderate and 3-severe). Full range from 0-10, higher score indicates more severity. Percent change in the LPPAI at Week 24 and Week 48 as compared to baseline.

Outcome measures

Outcome measures
Measure
PF-06651600 (Ritlecitinib)
n=50 Participants
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Percent Change in the Lichen Planopilaris Activity Index (LPPAI)
Week 24
-57.9 Percent change in score on a scale
Standard Error 5.9
Percent Change in the Lichen Planopilaris Activity Index (LPPAI)
Week 48
-69.9 Percent change in score on a scale
Standard Error 3.8

SECONDARY outcome

Timeframe: Baseline, Week 24 and Week 48

Population: Data results for participants who provided data at timepoints.

Percent change in Central Hair Loss Grade (CHLG) is an ordinal photographic outcome derived from a validated central scalp alopecia photographic scale to capture the pattern and severity of central hair loss. The scale uses standardized photographs and grades severity from 0 to 5, with 0 representing no hair loss, grades 1 and 2 representing early hair loss, and grades 3 to 5 representing probable CCCA with increasing severity.

Outcome measures

Outcome measures
Measure
PF-06651600 (Ritlecitinib)
n=50 Participants
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Percentage Change From Baseline in Change in Central Hair Loss Grade (CHLG)
Week 24
-24.4 Percent change in score on a scale
Standard Error 7.8
Percentage Change From Baseline in Change in Central Hair Loss Grade (CHLG)
Week 48
-46.9 Percent change in score on a scale
Standard Error 12.4

Adverse Events

PF-06651600 (Ritlecitinib)

Serious events: 0 serious events
Other events: 43 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
PF-06651600 (Ritlecitinib)
n=50 participants at risk
200 mg once-daily for 8 weeks and then 100 mg once daily for the remaining 40 weeks
Skin and Subcutaneous Tissue Disorders
Urticaria/Hives
2.0%
1/50 • 48 Weeks
Blood and Lymphatic System Disorders
Lymphopenia
28.0%
14/50 • 48 Weeks
Gastrointestinal Disorders
Elevated Liver Enzyme
4.0%
2/50 • 48 Weeks
Blood and Lymphatic System Disorders
Elevated AST
2.0%
1/50 • 48 Weeks
Blood and Lymphatic System Disorders
Decreased White Blood Cell Count
4.0%
2/50 • 48 Weeks
Blood and Lymphatic System Disorders
Anemia
4.0%
2/50 • 48 Weeks
Infections and Infestations
Oral Herpes Symplex
2.0%
1/50 • 48 Weeks
Infections and Infestations
Upper Respiratory Infection
4.0%
2/50 • 48 Weeks
Infections and Infestations
Nasopharyngitis
2.0%
1/50 • 48 Weeks
Blood and Lymphatic System Disorders
Elevated CPK
38.0%
19/50 • 48 Weeks
Blood and Lymphatic System Disorders
Leukopenia
12.0%
6/50 • 48 Weeks
Blood and Lymphatic System Disorders
Lymphocytopenia
16.0%
8/50 • 48 Weeks
Blood and Lymphatic System Disorders
Lymphocytopenia <500
4.0%
2/50 • 48 Weeks
Blood and Lymphatic System Disorders
Neutropenia
14.0%
7/50 • 48 Weeks
Blood and Lymphatic System Disorders
Neutropenia <1
2.0%
1/50 • 48 Weeks
Blood and Lymphatic System Disorders
Thrombocytopenia
4.0%
2/50 • 48 Weeks
General Disorders
Weight Gain
2.0%
1/50 • 48 Weeks
Ear and Labyrinth Disorders
Tinnitus
2.0%
1/50 • 48 Weeks
Gastrointestinal Disorders
Diarrrhea
4.0%
2/50 • 48 Weeks
General Disorders
Fatigue
10.0%
5/50 • 48 Weeks
General Disorders
Headaches
4.0%
2/50 • 48 Weeks
General Disorders
Restless Leg Syndrome
2.0%
1/50 • 48 Weeks
Renal and Urinary Disorders
Acute Kidney Injury
2.0%
1/50 • 48 Weeks
Skin and Subcutaneous Tissue Disorders
Acne
4.0%
2/50 • 48 Weeks

Additional Information

Giselle Singer

Icahn School of Medicine at Mount Sinai

Phone: 212-241-3288

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60