Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy
NCT05506254 · Status: ACTIVE_NOT_RECRUITING · Type: OBSERVATIONAL · Enrollment: 4
Last updated 2026-02-05
Summary
This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001
Conditions
- Methylmalonic Acidemia
Interventions
- DRUG
-
hLB-001
hLB-001 gene therapy
Sponsors & Collaborators
-
Alexion Pharmaceuticals, Inc.
lead INDUSTRY
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2022-07-15
- Primary Completion
- 2037-01-01
- Completion
- 2037-01-01
- FDA Drug
- Yes
Countries
- United States
Study Locations
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