Trial Outcomes & Findings for A Study to Evaluate Lumasiran in Adults With Recurrent Calcium Oxalate Kidney Stone Disease and Elevated Urinary Oxalate Levels (NCT NCT05161936)

NCT ID: NCT05161936

Last Updated: 2024-05-22

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

2 participants

Primary outcome timeframe

Baseline to Month 6

Results posted on

2024-05-22

Participant Flow

Participant milestones

Participant milestones
Measure
Lumasiran Dose 1
Participants will be administered lumasiran by subcutaneous (SC) injection. Lumasiran: Lumasiran will be administered by SC injection.
Lumasiran Dose 2
Participants will be administered lumasiran by SC injection. Lumasiran: Lumasiran will be administered by SC injection.
Placebo
Participants will be administered placebo by SC injection. Placebo: Placebo will be administered by SC injection.
Overall Study
STARTED
1
0
1
Overall Study
COMPLETED
0
0
0
Overall Study
NOT COMPLETED
1
0
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Lumasiran Dose 1
Participants will be administered lumasiran by subcutaneous (SC) injection. Lumasiran: Lumasiran will be administered by SC injection.
Lumasiran Dose 2
Participants will be administered lumasiran by SC injection. Lumasiran: Lumasiran will be administered by SC injection.
Placebo
Participants will be administered placebo by SC injection. Placebo: Placebo will be administered by SC injection.
Overall Study
Study terminated by Sponsor
1
0
0
Overall Study
Withdrawal by Subject
0
0
1

Baseline Characteristics

A Study to Evaluate Lumasiran in Adults With Recurrent Calcium Oxalate Kidney Stone Disease and Elevated Urinary Oxalate Levels

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Lumasiran Dose 1
n=1 Participants
Participants will be administered lumasiran by subcutaneous (SC) injection. Lumasiran: Lumasiran will be administered by SC injection.
Lumasiran Dose 2
Participants will be administered lumasiran by SC injection. Lumasiran: Lumasiran will be administered by SC injection.
Placebo
n=1 Participants
Participants will be administered placebo by SC injection. Placebo: Placebo will be administered by SC injection.
Total
n=2 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
Age, Categorical
Between 18 and 65 years
1 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
1 Participants
n=7 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
1 Participants
n=206 Participants
1 Participants
n=7 Participants
Age, Continuous
52 years
n=99 Participants
65 years
n=206 Participants
58.5 years
n=7 Participants
Sex: Female, Male
Female
1 Participants
n=99 Participants
0 Participants
n=206 Participants
1 Participants
n=7 Participants
Sex: Female, Male
Male
0 Participants
n=99 Participants
1 Participants
n=206 Participants
1 Participants
n=7 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
Race (NIH/OMB)
Asian
0 Participants
n=99 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=99 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
Race (NIH/OMB)
White
1 Participants
n=99 Participants
1 Participants
n=206 Participants
2 Participants
n=7 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
Region of Enrollment
Belgium
1 participants
n=99 Participants
0 participants
n=206 Participants
1 participants
n=7 Participants
Region of Enrollment
United States
0 participants
n=99 Participants
1 participants
n=206 Participants
1 participants
n=7 Participants
Region of Enrollment
Italy
0 participants
n=99 Participants
0 participants
n=206 Participants
0 participants
n=7 Participants
Region of Enrollment
United Kingdom
0 participants
n=99 Participants
0 participants
n=206 Participants
0 participants
n=7 Participants
Region of Enrollment
Switzerland
0 participants
n=99 Participants
0 participants
n=206 Participants
0 participants
n=7 Participants
Region of Enrollment
Spain
0 participants
n=99 Participants
0 participants
n=206 Participants
0 participants
n=7 Participants

PRIMARY outcome

Timeframe: Baseline to Month 6

Population: No participant data was collected for this outcome measure due to early study termination.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline to Month 6

Population: No participant data was collected for this outcome measure due to early study termination.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline to Month 6

Population: No participant data was collected for this outcome measure due to early study termination.

Outcome measures

Outcome data not reported

Adverse Events

Lumasiran Dose 1

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Lumasiran Dose 2

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Lumasiran Dose 1
n=1 participants at risk
Participants will be administered lumasiran by subcutaneous (SC) injection. Lumasiran: Lumasiran will be administered by SC injection.
Lumasiran Dose 2
Participants will be administered lumasiran by SC injection. Lumasiran: Lumasiran will be administered by SC injection.
Placebo
n=1 participants at risk
Participants will be administered placebo by SC injection. Placebo: Placebo will be administered by SC injection.
Metabolism and nutrition disorders
Type 2 Diabetes Mellitus
100.0%
1/1 • Number of events 1 • Up to 9 months
No participants were enrolled or treated with Lumasiran Dose 2.
0/0 • Up to 9 months
No participants were enrolled or treated with Lumasiran Dose 2.
0.00%
0/1 • Up to 9 months
No participants were enrolled or treated with Lumasiran Dose 2.
Respiratory, thoracic and mediastinal disorders
Cough
0.00%
0/1 • Up to 9 months
No participants were enrolled or treated with Lumasiran Dose 2.
0/0 • Up to 9 months
No participants were enrolled or treated with Lumasiran Dose 2.
100.0%
1/1 • Number of events 1 • Up to 9 months
No participants were enrolled or treated with Lumasiran Dose 2.

Additional Information

Chief Medical Officer

Alnylam Pharmaceuticals Inc.

Phone: 866-330-0326

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place