Trial Outcomes & Findings for DaxibotulinumtoxinA Injection for Treatment of Adductor Spasmodic Dysphonia (NCT NCT05158166)

NCT ID: NCT05158166

Last Updated: 2026-05-18

Results Overview

The Voice Handicap Index-10 (VHI-10) is a patient-reported questionnaire (range 0-40) that measures voice-related handicap, with higher scores indicating greater severity. Difference between baseline and 30 days post DAXI injection scores will be determined using a paired t-test with subjects pre-treatment VHI-10 scores as a control.

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

22 participants

Primary outcome timeframe

30 days

Results posted on

2026-05-18

Participant Flow

Participant milestones

Participant milestones
Measure
Administration of Daxi
Injectible daxibotulinumtoxinA (DAXI, Revance Therapeutics Inc., Newark, CA) is an investigational botulinum toxin type A which has been shown in large clinical trials to provide safe, effective treatment for glabellar lines and cervical dystonia and may offer longer-lasting results when compared with onabotulinumtoxinA. Dosage will be same number of units as prior Botox A dose.
Overall Study
STARTED
22
Overall Study
COMPLETED
22
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

DaxibotulinumtoxinA Injection for Treatment of Adductor Spasmodic Dysphonia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Administration of Daxi
n=20 Participants
Injectible daxibotulinumtoxinA (DAXI, Revance Therapeutics Inc., Newark, CA) is an investigational botulinum toxin type A which has been shown in large clinical trials to provide safe, effective treatment for glabellar lines and cervical dystonia and may offer longer-lasting results when compared with onabotulinumtoxinA. Dosage will be same number of units as prior Botox A dose.
Age, Continuous
58.3 Years
n=11 Participants
Sex: Female, Male
Female
15 Participants
n=11 Participants
Sex: Female, Male
Male
5 Participants
n=11 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=11 Participants
Race (NIH/OMB)
Asian
0 Participants
n=11 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=11 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=11 Participants
Race (NIH/OMB)
White
18 Participants
n=11 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=11 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=11 Participants
VHI-10
21.10 units on a scale
STANDARD_DEVIATION 6.82 • n=11 Participants

PRIMARY outcome

Timeframe: 30 days

Population: Two patients had no change in their voice and no swallowing impact. These patients were thus considered "misses," or injection events that did not reach the intended TA-LCA muscle complexes and thus were not included in the subsequent analysis.

The Voice Handicap Index-10 (VHI-10) is a patient-reported questionnaire (range 0-40) that measures voice-related handicap, with higher scores indicating greater severity. Difference between baseline and 30 days post DAXI injection scores will be determined using a paired t-test with subjects pre-treatment VHI-10 scores as a control.

Outcome measures

Outcome measures
Measure
Administration of Daxi
n=20 Participants
Injectible daxibotulinumtoxinA (DAXI, Revance Therapeutics Inc., Newark, CA) is an investigational botulinum toxin type A which has been shown in large clinical trials to provide safe, effective treatment for glabellar lines and cervical dystonia and may offer longer-lasting results when compared with onabotulinumtoxinA. Dosage will be same number of units as prior Botox A dose.
Our Primary Outcome is the Difference in VHI-10 Score at 30 Days After Injection With DAXI.
17.81 units on a scale
Standard Deviation 8.18

SECONDARY outcome

Timeframe: Up to 1 year

Population: Two patients had no change in their voice and no swallowing impact. These patients were thus considered "misses," or injection events that did not reach the intended TA-LCA muscle complexes and thus were not included in the subsequent analysis. The overall cohort was split into three subgroups based on their Duration of Voice Benefit (DVB) with DAXI and Botox (BtxA) for statistical analysis: Group A (DVB DAXI\>BtxA), Group B (DVB DAXI=BtxA), and Group C (DVB DAXI\<BtxA)

Duration of Voice Benefit (DVB) was determined by calculating the difference of time (in days) between injection date and time the patient reported a significant reduction of benefit that would prompt scheduling a repeat treatment. DVB is routinely calculated for all Adductor-type laryngeal dystonia (AdLD) patients during their return visits by asking "how many days ago did you lose injection benefit such that you felt you needed another injection." This time frame was then subtracted from the number of days between injection dates to calculate DVB. For Botox (BtxA), a mean DVB was calculated by averaging the last three DVB values from successful injections to compare to the Daxi DVB. Clinically significant difference in DVB was a priori determined as \> 14 days between values to allow for normal inter-injection variability.

Outcome measures

Outcome measures
Measure
Administration of Daxi
n=20 Participants
Injectible daxibotulinumtoxinA (DAXI, Revance Therapeutics Inc., Newark, CA) is an investigational botulinum toxin type A which has been shown in large clinical trials to provide safe, effective treatment for glabellar lines and cervical dystonia and may offer longer-lasting results when compared with onabotulinumtoxinA. Dosage will be same number of units as prior Botox A dose.
A Secondary Outcome Will be Comparing the Duration of Effect of DAXI With Patients' Prior Botox Treatment.
Group A (DVB DAXI>BtxA) Mean DVB for Daxi
130.6 days
Interval 34.0 to 179.0
A Secondary Outcome Will be Comparing the Duration of Effect of DAXI With Patients' Prior Botox Treatment.
Group A (DVB DAXI>BtxA) Mean DVB for BtxA
86.1 days
Interval 51.0 to 111.0
A Secondary Outcome Will be Comparing the Duration of Effect of DAXI With Patients' Prior Botox Treatment.
Group B (DVB DAXI=BtxA) Mean DVB for Daxi
86.86 days
Interval 69.0 to 118.0
A Secondary Outcome Will be Comparing the Duration of Effect of DAXI With Patients' Prior Botox Treatment.
Group B (DVB DAXI=BtxA) Mean DVB for BtxA
83.29 days
Interval 70.0 to 111.0
A Secondary Outcome Will be Comparing the Duration of Effect of DAXI With Patients' Prior Botox Treatment.
Group C (DVB DAXI<BtxA) Mean DVB for DAXI
49.8 days
Interval 37.0 to 66.0
A Secondary Outcome Will be Comparing the Duration of Effect of DAXI With Patients' Prior Botox Treatment.
Group C (DVB DAXI<BtxA) Mean DVB for BtxA
81.8 days
Interval 52.0 to 92.0

Adverse Events

Administration of Daxi

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Clark Rosen

University of California, San Francisco

Phone: (415)-885-7700

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place