Trial Outcomes & Findings for BEMPEG With Pembrolizumab vs Pembrolizumab Alone in Patients With Metastatic or Recurrent HNSCC (PROPEL-36) (NCT NCT04969861)

NCT ID: NCT04969861

Last Updated: 2023-01-12

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE2/PHASE3

Target enrollment

1 participants

Primary outcome timeframe

Approximately 2 years

Results posted on

2023-01-12

Participant Flow

Participant milestones

Participant milestones
Measure
BEMPEG + Pembrolizumab
Bempegaldesleukin plus pembrolizumab every 3 weeks (q3w) for up to 35 cycles (approximately 2 years). Bempegaldesleukin: Specified dose on specified days Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Pembrolizumab Monotherapy
Pembrolizumab monotherapy q3w for up to 35 cycles (approximately 2 years). Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Overall Study
STARTED
1
0
Overall Study
COMPLETED
0
0
Overall Study
NOT COMPLETED
1
0

Reasons for withdrawal

Reasons for withdrawal
Measure
BEMPEG + Pembrolizumab
Bempegaldesleukin plus pembrolizumab every 3 weeks (q3w) for up to 35 cycles (approximately 2 years). Bempegaldesleukin: Specified dose on specified days Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Pembrolizumab Monotherapy
Pembrolizumab monotherapy q3w for up to 35 cycles (approximately 2 years). Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Overall Study
Study was terminated in consonance with discontinuation of bempegaldesleukin program.
1
0

Baseline Characteristics

BEMPEG With Pembrolizumab vs Pembrolizumab Alone in Patients With Metastatic or Recurrent HNSCC (PROPEL-36)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
BEMPEG + Pembrolizumab
n=1 Participants
Bempegaldesleukin plus pembrolizumab every 3 weeks (q3w) for up to 35 cycles (approximately 2 years). Bempegaldesleukin: Specified dose on specified days Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Pembrolizumab Monotherapy
Pembrolizumab monotherapy q3w for up to 35 cycles (approximately 2 years). Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Total
n=1 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Age, Categorical
>=65 years
1 Participants
n=99 Participants
1 Participants
n=206 Participants
Age, Continuous
69 years
n=99 Participants
69 years
n=206 Participants
Sex: Female, Male
Female
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Sex: Female, Male
Male
1 Participants
n=99 Participants
1 Participants
n=206 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Asian
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
White
1 Participants
n=99 Participants
1 Participants
n=206 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
0 Participants
n=206 Participants
Region of Enrollment
Austria
0 participants
n=99 Participants
0 participants
n=206 Participants
Region of Enrollment
Greece
0 participants
n=99 Participants
0 participants
n=206 Participants
Region of Enrollment
United States
1 participants
n=99 Participants
1 participants
n=206 Participants
Region of Enrollment
Italy
0 participants
n=99 Participants
0 participants
n=206 Participants

PRIMARY outcome

Timeframe: Approximately 2 years

Population: Nektar and BMS Study PIVOT-IO-001 did not meet its primary EP of demonstrating an efficacy advantage from addition of BEMPEG to nivolumab in patients with previously untreated inoperable or metastatic melanoma. PIVOT-09 (RCC) and PIVOT-10 (uroth C) studies also reported negative topline results. Based on these 3 large negative studies, Nektar and SFJ in consultation with the study IDMC made the decision to discontinue this trial. At termination, 1 patient was enrolled and treated for 2 cycles.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: Approximately 2 years

To compare the objective response rate (ORR) of bempegaldesleukin plus pembrolizumab versus pembrolizumab monotherapy.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Approximately 2 years

To compare progression-free survival (PFS) of bempegaldesleukin plus pembrolizumab versus pembrolizumab monotherapy.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Approximately 2 years

The time from baseline to a ≥ 10-point decrease with confirmation by the subsequent visit of a ≥ 10-point deterioration from baseline in: • Global health status/quality of life assessment based on the European Organization for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire-Core 30 (QLQ-C30). The EORTC QLQ-C30 is a 30-item questionnaire designed to assess the quality of life of cancer patients. All scale scores are linearly converted to range from 0 to 100. A higher total score indicates a better level of functioning. • Pain and Swallowing based on respective multi-item scales of EORTC QLQ head and neck cancer specific module (EORTC QLQ-H\&N35). EORTC QLQ-H\&N35 consists of 7 multi-item scales that assess pain, swallowing, senses, speech, social eating, social contact and sexuality. All scale scores are linearly converted to range from 0 to 100. A higher total score indicates increased severity of symptoms.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Approximately 2 years

To compare mean change from baseline in global health status/quality of life scale of EORTC QLQ-C30. The EORTC QLQ-C30 is composed of multi-item scales and single item measures. These include 5 functional scales (physical, role, emotional, cognitive, and social), 3 symptom scales (fatigue, nausea/vomiting, and pain), a global health status/HRQoL scale, and 6 single items (dyspnea, insomnia, appetite loss, constipation, diarrhea, and financial difficulties). Each of the multi-item scales includes a different set of items - no item occurs in more than one scale. All scale scores are linearly converted to range from 0 to 100. A higher total score indicates a better level of functioning.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Screening baseline through end of study, approximately 2 years

Compare the overall safety and tolerability based on assessments of treatment-emergent adverse events and serious adverse events

Outcome measures

Outcome data not reported

Adverse Events

BEMPEG + Pembrolizumab

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Pembrolizumab Monotherapy

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
BEMPEG + Pembrolizumab
n=1 participants at risk
Bempegaldesleukin plus pembrolizumab every 3 weeks (q3w) for up to 35 cycles (approximately 2 years). Bempegaldesleukin: Specified dose on specified days Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Pembrolizumab Monotherapy
Pembrolizumab monotherapy q3w for up to 35 cycles (approximately 2 years). Pembrolizumab: Pembrolizumab (anti-PD-1) will be dosed as per the pharmacy manual.
Respiratory, thoracic and mediastinal disorders
Cough
100.0%
1/1 • Number of events 1 • 1 month
There were no SAEs, no mortalities. In total, one Grade 1 AE of cough was reported.
0/0 • 1 month
There were no SAEs, no mortalities. In total, one Grade 1 AE of cough was reported.

Additional Information

Study Director

Nektar Therapeutics

Phone: 415-482-5300

Results disclosure agreements

  • Principal investigator is a sponsor employee There are restrictions to the PI's rights to discuss or publish trial results.
  • Publication restrictions are in place

Restriction type: OTHER