A Prospective Clinical Study of Phenylketonuria (PKU)
NCT04452513 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 32
Last updated 2023-03-14
Summary
This is a study for adults and children ≥ 14 years old who have Phenylketonuria (PKU) with uncontrolled plasma Phe levels. No clinical intervention or study drug is provided by BioMarin in this study.
Conditions
- Phenylketonurias
Sponsors & Collaborators
- lead INDUSTRY
Eligibility
- Min Age
- 14 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2019-10-11
- Primary Completion
- 2022-06-02
- Completion
- 2022-06-02
Countries
- United States
Study Locations
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