Trial Outcomes & Findings for Anti-neutrophil Cytoplasmic Antibody in Interstitial Lung Disease. (NCT NCT04413149)

NCT ID: NCT04413149

Last Updated: 2024-05-17

Results Overview

Death from all causes Retrieved from medical records.

Recruitment status

COMPLETED

Target enrollment

80 participants

Primary outcome timeframe

From baseline until the date of death from all cause, up to 5 years

Results posted on

2024-05-17

Participant Flow

Participant milestones

Participant milestones
Measure
MPA-ILD Group
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Overall Study
STARTED
31
49
Overall Study
COMPLETED
20
44
Overall Study
NOT COMPLETED
11
5

Reasons for withdrawal

Reasons for withdrawal
Measure
MPA-ILD Group
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Overall Study
Death
10
5
Overall Study
Lung transplantation
1
0

Baseline Characteristics

Anti-neutrophil Cytoplasmic Antibody in Interstitial Lung Disease.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
MPA-ILD Group
n=31 Participants
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
n=49 Participants
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Total
n=80 Participants
Total of all reporting groups
Age, Continuous
62 years
n=99 Participants
59 years
n=107 Participants
60 years
n=206 Participants
Sex: Female, Male
Female
19 Participants
n=99 Participants
25 Participants
n=107 Participants
44 Participants
n=206 Participants
Sex: Female, Male
Male
12 Participants
n=99 Participants
24 Participants
n=107 Participants
36 Participants
n=206 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Asian
31 Participants
n=99 Participants
49 Participants
n=107 Participants
80 Participants
n=206 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
White
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Region of Enrollment
China
31 participants
n=99 Participants
49 participants
n=107 Participants
80 participants
n=206 Participants
Follow-up time
36 months
n=99 Participants
41 months
n=107 Participants
40 months
n=206 Participants
Fever
16 Participants
n=99 Participants
10 Participants
n=107 Participants
26 Participants
n=206 Participants
Cough
28 Participants
n=99 Participants
42 Participants
n=107 Participants
70 Participants
n=206 Participants
Dyspnea
20 Participants
n=99 Participants
29 Participants
n=107 Participants
49 Participants
n=206 Participants
Fatigue
6 Participants
n=99 Participants
5 Participants
n=107 Participants
11 Participants
n=206 Participants
Arthralgia
8 Participants
n=99 Participants
15 Participants
n=107 Participants
23 Participants
n=206 Participants
Crackling sound
19 Participants
n=99 Participants
26 Participants
n=107 Participants
45 Participants
n=206 Participants
Rash
3 Participants
n=99 Participants
7 Participants
n=107 Participants
10 Participants
n=206 Participants
Clubbing fingers
5 Participants
n=99 Participants
2 Participants
n=107 Participants
7 Participants
n=206 Participants
Mechanics hand
0 Participants
n=99 Participants
2 Participants
n=107 Participants
2 Participants
n=206 Participants
Gottron's sign
1 Participants
n=99 Participants
2 Participants
n=107 Participants
3 Participants
n=206 Participants
Renal involvement
30 Participants
n=99 Participants
0 Participants
n=107 Participants
30 Participants
n=206 Participants
Nervous system involvement
3 Participants
n=99 Participants
0 Participants
n=107 Participants
3 Participants
n=206 Participants
Cardiovascular involvement
2 Participants
n=99 Participants
0 Participants
n=107 Participants
2 Participants
n=206 Participants
Retinal involvement
1 Participants
n=99 Participants
0 Participants
n=107 Participants
1 Participants
n=206 Participants
White blood cell
9.34 ×10^9 cells/L
n=99 Participants
7.44 ×10^9 cells/L
n=107 Participants
8.54 ×10^9 cells/L
n=206 Participants
Neutrophil
6.79 ×10^9 cells/L
n=99 Participants
4.68 ×10^9 cells/L
n=107 Participants
5.65 ×10^9 cells/L
n=206 Participants
Lymphocyte
1.47 ×10^9 cells/L
n=99 Participants
2 ×10^9 cells/L
n=107 Participants
1.90 ×10^9 cells/L
n=206 Participants
Hemoglobin
116 g/L
n=99 Participants
137 g/L
n=107 Participants
132 g/L
n=206 Participants
Platelet
251 ×10^9 cells/L
n=99 Participants
234 ×10^9 cells/L
n=107 Participants
246 ×10^9 cells/L
n=206 Participants
Erythrocyte sedimentation rate
86 mm/h
n=99 Participants
28 mm/h
n=107 Participants
53 mm/h
n=206 Participants
C reactive protein
35.77 mg/dL
n=99 Participants
13.87 mg/dL
n=107 Participants
15.92 mg/dL
n=206 Participants
PaO2
71.5 mmHg
n=99 Participants
77.4 mmHg
n=107 Participants
75.9 mmHg
n=206 Participants
Creatinine
73 μmol/L
n=99 Participants
67 μmol/L
n=107 Participants
68 μmol/L
n=206 Participants
MPO-ANCA positive
26 Participants
n=99 Participants
19 Participants
n=107 Participants
45 Participants
n=206 Participants
PR3-ANCA positive
0 Participants
n=99 Participants
2 Participants
n=107 Participants
2 Participants
n=206 Participants
Rheumatoid factor
113.1 IU/mL
n=99 Participants
26.7 IU/mL
n=107 Participants
55.9 IU/mL
n=206 Participants
ANA positive
15 Participants
n=99 Participants
30 Participants
n=107 Participants
45 Participants
n=206 Participants
Anti-CCP positive
0 Participants
n=99 Participants
8 Participants
n=107 Participants
8 Participants
n=206 Participants
SSA positive
3 Participants
n=99 Participants
6 Participants
n=107 Participants
9 Participants
n=206 Participants
SSB positive
2 Participants
n=99 Participants
2 Participants
n=107 Participants
4 Participants
n=206 Participants
Jo-1 positive
0 Participants
n=99 Participants
1 Participants
n=107 Participants
1 Participants
n=206 Participants
Scl-70 positive
1 Participants
n=99 Participants
1 Participants
n=107 Participants
2 Participants
n=206 Participants
FEV1
79.36 percent predicted
STANDARD_DEVIATION 17.92 • n=99 Participants
84.03 percent predicted
STANDARD_DEVIATION 16.93 • n=107 Participants
82.35 percent predicted
STANDARD_DEVIATION 17.32 • n=206 Participants
FVC
78.30 percent predicted
STANDARD_DEVIATION 16.89 • n=99 Participants
83.84 percent predicted
STANDARD_DEVIATION 19.10 • n=107 Participants
81.85 percent predicted
STANDARD_DEVIATION 18.42 • n=206 Participants
TLC
74.16 percent predicted
STANDARD_DEVIATION 12.73 • n=99 Participants
79.53 percent predicted
STANDARD_DEVIATION 13.55 • n=107 Participants
77.59 percent predicted
STANDARD_DEVIATION 13.43 • n=206 Participants
DLCO
56.56 percent predicted
STANDARD_DEVIATION 17.52 • n=99 Participants
62.12 percent predicted
STANDARD_DEVIATION 14.09 • n=107 Participants
60.12 percent predicted
STANDARD_DEVIATION 15.53 • n=206 Participants
Ground-glass opacity
25 Participants
n=99 Participants
44 Participants
n=107 Participants
69 Participants
n=206 Participants
Consolidation
4 Participants
n=99 Participants
4 Participants
n=107 Participants
8 Participants
n=206 Participants
Traction bronchiectasis
16 Participants
n=99 Participants
20 Participants
n=107 Participants
36 Participants
n=206 Participants
Honeycombing
11 Participants
n=99 Participants
8 Participants
n=107 Participants
19 Participants
n=206 Participants
Pulmonary artery dilation
3 Participants
n=99 Participants
1 Participants
n=107 Participants
4 Participants
n=206 Participants
Reticular pattern
20 Participants
n=99 Participants
29 Participants
n=107 Participants
49 Participants
n=206 Participants
Curved linear opacity
5 Participants
n=99 Participants
12 Participants
n=107 Participants
17 Participants
n=206 Participants
Pleural thickening
4 Participants
n=99 Participants
9 Participants
n=107 Participants
13 Participants
n=206 Participants
Interlobular septal thickening
16 Participants
n=99 Participants
23 Participants
n=107 Participants
39 Participants
n=206 Participants
Micronodular pattern
5 Participants
n=99 Participants
6 Participants
n=107 Participants
11 Participants
n=206 Participants
Subpleural bulla
10 Participants
n=99 Participants
10 Participants
n=107 Participants
20 Participants
n=206 Participants
Enlarged mediastinal lymph node
2 Participants
n=99 Participants
3 Participants
n=107 Participants
5 Participants
n=206 Participants
Usual interstitial pneumonia
4 Participants
n=99 Participants
3 Participants
n=107 Participants
7 Participants
n=206 Participants
Nonspecific interstitial pneumonia
18 Participants
n=99 Participants
33 Participants
n=107 Participants
51 Participants
n=206 Participants
Unclassifiable HRCT pattern
9 Participants
n=99 Participants
13 Participants
n=107 Participants
22 Participants
n=206 Participants

PRIMARY outcome

Timeframe: From baseline until the date of death from all cause, up to 5 years

Death from all causes Retrieved from medical records.

Outcome measures

Outcome measures
Measure
MPA-ILD Group
n=31 Participants
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
n=49 Participants
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Death From All Causes
10 Participants
5 Participants

PRIMARY outcome

Timeframe: From baseline until the date of transplantation, up to 5 years

Number of patients who underwent lung transplantation Retrieved from medical records.

Outcome measures

Outcome measures
Measure
MPA-ILD Group
n=31 Participants
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
n=49 Participants
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Number of Patients Who Underwent Lung Transplantation
1 Participants
0 Participants

Adverse Events

MPA-ILD Group

Serious events: 0 serious events
Other events: 0 other events
Deaths: 10 deaths

ANCA-IIP Group

Serious events: 0 serious events
Other events: 0 other events
Deaths: 5 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr. Shi Juhong

Peking Union Medical College Hospital

Phone: +86-13701178492

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place