A Study of YVOIRE Y-Solution 360 for Hand Augmentation to Correct Volume Loss

Oscillation and Lung Expansion (OLE) Therapy for Treatment of Neuromuscular Disease (NMD) Patients

NCT05366010 ·Status: TERMINATED ·Phase: NA

A Study of the Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients with Gaucher Disease Type I

NCT06162338 ·Status: RECRUITING ·Phase: NA

Your Voice; Impact of Duchenne Muscular Dystrophy (DMD) on the Lives of Families

NCT03680365 ·Status: COMPLETED

Determine the Safety and Dose of EN001 in Patients With Duchenne Muscular Dystrophy(DMD)

NCT05338099 ·Status: COMPLETED ·Phase: PHASE1

Safety/Efficacy Study for the Treatment of Amyotrophic Lateral Sclerosis

NCT01082653 ·Status: SUSPENDED ·Phase: PHASE1

An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy

NCT04708314 ·Status: TERMINATED ·Phase: PHASE4

Trial of Autologous Mesenchymal Stem Cells in Patients With Multiple System Atrophy

NCT00911365 ·Status: COMPLETED ·Phase: PHASE2

A Trial of Chronotherapy of Corticosteroids in Duchenne Muscular Dystrophy

NCT02036463 ·Status: WITHDRAWN ·Phase: PHASE2

A Phase I Open Label Dose Escalation Trial of RNA-144101 in the Treatment of Geographic Atrophy

NCT01093170 ·Status: WITHDRAWN ·Phase: PHASE1

Evaluate the Efficacy and Safety of EN001 in Patients With Duchenne Muscular Dystrophy

NCT06328725 ·Status: NOT_YET_RECRUITING ·Phase: PHASE1/PHASE2

Safety and Efficacy Study of Autologous Bone Marrow Derived Stem Cell Treatment in Amyotrophic Lateral Sclerosis

NCT01363401 ·Status: COMPLETED ·Phase: PHASE1/PHASE2

A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)

NCT06114056 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1

Evaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular Atrophy

NCT06562283 ·Status: RECRUITING ·Phase: NA

A Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher Disease

NCT06818838 ·Status: RECRUITING ·Phase: PHASE1/PHASE2

External Pharyngeal Exerciser and Dysphagia

NCT05708898 ·Status: RECRUITING ·Phase: NA

Prognostic Value of a Diaphragmatic Endurance Test in Patients With Amyotrophic Lateral Sclerosis

NCT02528071 ·Status: TERMINATED

Nerve Growth Factor Encapsulated With 2-methacryloyloxyethyl Phosphorylcholine Nanocapsules in the Treatment of Amyotrophic Lateral Sclerosis

NCT06391645 ·Status: NOT_YET_RECRUITING ·Phase: PHASE2/PHASE3

Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2

NCT02484560 ·Status: UNKNOWN ·Phase: PHASE1

Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease

NCT02574286 ·Status: COMPLETED ·Phase: PHASE4

A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

NCT03406780 ·Status: COMPLETED ·Phase: PHASE2

Evaluate the Safety and Potential Efficacy of Human Wharton's Jelly-derived Mesenchymal Stem Cells With Charcot-Marie-Tooth Disease Type 1E

NCT06218134 ·Status: COMPLETED ·Phase: NA

NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

NCT05996003 ·Status: RECRUITING ·Phase: PHASE2

A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular Dystrophy

NCT02310763 ·Status: TERMINATED ·Phase: PHASE2

Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy

NCT04281485 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE3

This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular Dystrophy

NCT01098708 ·Status: COMPLETED