Trial Outcomes & Findings for Study of the Safety and Tolerability of AXA1957 in Adolescent Subjects With Non-Alcoholic Fatty Liver Disease (NAFLD) (NCT NCT04073407)

NCT ID: NCT04073407

Last Updated: 2021-09-23

Results Overview

Study food product emergent adverse events (AEs). Subjects reporting \>or equal to 1 study food product-emergent AE.

Recruitment status

TERMINATED

Study phase

NA

Target enrollment

9 participants

Primary outcome timeframe

AEs Baseline to week 13 - Part 1

Results posted on

2021-09-23

Participant Flow

Participant milestones

Participant milestones
Measure
AXA1957
AXA1957 20.4g AXA1957: Amino acids, food study
Placebo
Placebo 24g Placebo: placebo
Part 1
STARTED
6
3
Part 1
COMPLETED
1
2
Part 1
NOT COMPLETED
5
1
Part 2
STARTED
0
1
Part 2
COMPLETED
0
0
Part 2
NOT COMPLETED
0
1

Reasons for withdrawal

Reasons for withdrawal
Measure
AXA1957
AXA1957 20.4g AXA1957: Amino acids, food study
Placebo
Placebo 24g Placebo: placebo
Part 1
Withdrawal by Subject
1
0
Part 1
Subjects discontinued in response to restrictions on the study due to impact of COVID-19 pandemic
4
1
Part 2
Withdrawal by Subject
0
1

Baseline Characteristics

Study of the Safety and Tolerability of AXA1957 in Adolescent Subjects With Non-Alcoholic Fatty Liver Disease (NAFLD)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
AXA1957
n=6 Participants
AXA1957 20.4g AXA1957: Amino acids, food study
Placebo
n=3 Participants
Placebo 24g Placebo: placebo
Total
n=9 Participants
Total of all reporting groups
Age, Categorical
<=18 years
6 Participants
n=99 Participants
3 Participants
n=107 Participants
9 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Continuous
13.5 years
STANDARD_DEVIATION 1.38 • n=99 Participants
13.7 years
STANDARD_DEVIATION 1.15 • n=107 Participants
13.6 years
STANDARD_DEVIATION 1.24 • n=206 Participants
Sex: Female, Male
Female
3 Participants
n=99 Participants
1 Participants
n=107 Participants
4 Participants
n=206 Participants
Sex: Female, Male
Male
3 Participants
n=99 Participants
2 Participants
n=107 Participants
5 Participants
n=206 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Asian
1 Participants
n=99 Participants
1 Participants
n=107 Participants
2 Participants
n=206 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
White
5 Participants
n=99 Participants
2 Participants
n=107 Participants
7 Participants
n=206 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Region of Enrollment
United Kingdom
6 Participants
n=99 Participants
3 Participants
n=107 Participants
9 Participants
n=206 Participants

PRIMARY outcome

Timeframe: AEs Baseline to week 13 - Part 1

Population: Safety analysis for Part 1 Baseline to week 13

Study food product emergent adverse events (AEs). Subjects reporting \>or equal to 1 study food product-emergent AE.

Outcome measures

Outcome measures
Measure
AXA1957
n=6 Participants
AXA1957 20.4g AXA1957: Amino acids, food study
Placebo
n=3 Participants
Placebo 24g Placebo: placebo
Number of Subjects With Adverse Events (AEs).
2 Participants
1 Participants

Adverse Events

AXA1957

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
AXA1957
n=6 participants at risk
AXA1957 20.4g AXA1957: Amino acids, food study
Placebo
n=3 participants at risk
Placebo 24g Placebo: placebo
Gastrointestinal disorders
Abdominal pain
16.7%
1/6 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
0.00%
0/3 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
Gastrointestinal disorders
Vomiting
16.7%
1/6 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
33.3%
1/3 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
Gastrointestinal disorders
Abdominal pain upper
0.00%
0/6 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
33.3%
1/3 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
Gastrointestinal disorders
Nausea
0.00%
0/6 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
33.3%
1/3 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
Infections and infestations
Upper respiratory tract infection
16.7%
1/6 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
0.00%
0/3 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
Nervous system disorders
Headache
16.7%
1/6 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
33.3%
1/3 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
Nervous system disorders
Migraine
0.00%
0/6 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
33.3%
1/3 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
Nervous system disorders
Dizziness
0.00%
0/6 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.
33.3%
1/3 • Number of events 1 • From the time of informed consent up to first administration of study product on Day 1, any untoward medical occurrence considered related to study procedures will be recorded as an AE. Adverse events that occur from the first administration of study product on Day 1 through Week 13 (Part 1) and through Week 27 / Follow-up (Part 2 / Optional) will be considered treatment-emergent AEs.

Additional Information

Margaret Koziel, MD

Axcella Health, Inc

Phone: 8573202200

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place