Expanded Access Protocol of Givosiran for Patients With Acute Hepatic Porphyria
NCT04056481 · Status: APPROVED_FOR_MARKETING · Type: EXPANDED_ACCESS
Last updated 2024-05-20
Summary
The purpose of this study is to provide expanded access of givosiran to patients with Acute Hepatic Porphyria (AHP).
Conditions
- Acute Hepatic Porphyria
Interventions
- DRUG
-
Givosiran
givosiran (ALN-AS1) administered as a subcutaneous (SC) injection
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Medical Director · Alnylam Pharmaceuticals
Eligibility
- Min Age
- 12 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
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