Trial Outcomes & Findings for Screening for Cardiac Amyloidosis With Nuclear Imaging for Minority Populations (NCT NCT03812172)

NCT ID: NCT03812172

Last Updated: 2025-11-19

Results Overview

The prevalence of ATTR cardiac amyloidosis was calculated from among the number of subjects within the cohort determined to be ATTR-CA positive. Determination of ATTR-CA was defined as significant myocardial retention of Tc-99 PYP. The prevalence is expressed as a percentage of total enrollment. ATTR-CA prevalence is reported for two different groups: Self-identified as Black, subjects with Heart Failure and Self-identified as non-Black, subjects with Heart Failure.

Recruitment status

COMPLETED

Target enrollment

646 participants

Primary outcome timeframe

Study Participation of One Year

Results posted on

2025-11-19

Participant Flow

Black and Hispanic Caribbean patients with heart failure were recruited from North Manhattan (NYP West and Harlem Hospitals), Boston and New Haven via academic research facilities at Columbia University Irving Medical Center, Boston Medical Center and Yale/New Haven Health Center from 5-19-2019 until 6-12-2024

Participant milestones

Participant milestones
Measure
Self-Identified Black Race Participants With Heart Failure
ATTR-CA prevalence among subjects with heart failure self-identified as Black within predefined categories, (i.e., overall, men, women, Hispanic ethnicity age ≤75 and age \>75) Transthyretin cardiac amyloidosis status was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy. Those with transthyretin cardiac amyloidosis were further subtyped into those with a genetic cause (ATTRv) variant transthyretin cardiac amyloidosis and those with a non-genetic cause (ATTRwt - wild-type transthyretin cardiac amyloidosis).
Self-identified Non-Black Participants With Heart Failure:
ATTR-CA prevalence among subjects with heart failure not self-identified as Black within predefined categories, (i.e., overall, men, women, Hispanic ethnicity age ≤75 and age \>75) Transthyretin cardiac amyloidosis status was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy. Those with transthyretin cardiac amyloidosis were further subtyped into those with a genetic cause (ATTRv) variant transthyretin cardiac amyloidosis and those with a non-genetic cause (ATTRwt - wild-type transthyretin cardiac amyloidosis).
Overall Study
STARTED
550
96
Overall Study
COMPLETED
550
96
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Screening for Cardiac Amyloidosis With Nuclear Imaging for Minority Populations

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Self-Identified as Black, Subjects With Heart Failure
n=550 Participants
ATTR-CA prevalence among subjects with heart failure self-identified as Black within predefined categories, (i.e., overall, men, women, Hispanic ethnicity age ≤75 and age \>75) Transthyretin cardiac amyloidosis status was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy. Those with transthyretin cardiac amyloidosis were further subtyped into those with a genetic cause (ATTRv - variant transthyretin cardiac amyloidosis) and those with a non-genetic cause (ATTRwt - wild-type transthyretin cardiac amyloidosis).
Self-identified as Non-Black, Subjects With Heart Failure
n=96 Participants
ATTR-CA prevalence among subjects with heart failure not self-identified as Black within predefined categories, (i.e., overall, men, women, Hispanic ethnicity age ≤75 and age \>75) Transthyretin cardiac amyloidosis status was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy. Those with transthyretin cardiac amyloidosis were further subtyped into those with a genetic cause (ATTRv - variant transthyretin cardiac amyloidosis) and those with a non-genetic cause (ATTRwt - wild-type transthyretin cardiac amyloidosis).
Total
n=646 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=39 Participants
0 Participants
n=29 Participants
0 Participants
n=60 Participants
Age, Categorical
Between 18 and 65 years
118 Participants
n=39 Participants
16 Participants
n=29 Participants
134 Participants
n=60 Participants
Age, Categorical
>=65 years
432 Participants
n=39 Participants
80 Participants
n=29 Participants
512 Participants
n=60 Participants
Sex: Female, Male
Female
282 Participants
n=39 Participants
45 Participants
n=29 Participants
327 Participants
n=60 Participants
Sex: Female, Male
Male
268 Participants
n=39 Participants
51 Participants
n=29 Participants
319 Participants
n=60 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
90 Participants
n=39 Participants
96 Participants
n=29 Participants
186 Participants
n=60 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
460 Participants
n=39 Participants
0 Participants
n=29 Participants
460 Participants
n=60 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=39 Participants
0 Participants
n=29 Participants
0 Participants
n=60 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=39 Participants
0 Participants
n=29 Participants
0 Participants
n=60 Participants
Race (NIH/OMB)
Asian
0 Participants
n=39 Participants
1 Participants
n=29 Participants
1 Participants
n=60 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=39 Participants
0 Participants
n=29 Participants
0 Participants
n=60 Participants
Race (NIH/OMB)
Black or African American
547 Participants
n=39 Participants
0 Participants
n=29 Participants
547 Participants
n=60 Participants
Race (NIH/OMB)
White
0 Participants
n=39 Participants
12 Participants
n=29 Participants
12 Participants
n=60 Participants
Race (NIH/OMB)
More than one race
3 Participants
n=39 Participants
0 Participants
n=29 Participants
3 Participants
n=60 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=39 Participants
83 Participants
n=29 Participants
83 Participants
n=60 Participants

PRIMARY outcome

Timeframe: Study Participation of One Year

The prevalence of ATTR cardiac amyloidosis was calculated from among the number of subjects within the cohort determined to be ATTR-CA positive. Determination of ATTR-CA was defined as significant myocardial retention of Tc-99 PYP. The prevalence is expressed as a percentage of total enrollment. ATTR-CA prevalence is reported for two different groups: Self-identified as Black, subjects with Heart Failure and Self-identified as non-Black, subjects with Heart Failure.

Outcome measures

Outcome measures
Measure
Self-identified as Black, Subjects With Heart Failure
n=550 Participants
ATTR-CA prevalence, among subjects with heart failure who self-identified as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Self-identified as Non-Black, Subjects With Heart Failure
n=96 Participants
ATTR-CA prevalence, among subjects with heart failure who did not self-identify as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Prevalence of Transthyretin Cardiac Amyloidosis (ATTR-CA) in Cohort of Caribbean Hispanics and Blacks With Heart Failure (HF)
7.8 percentage of participants
0 percentage of participants

PRIMARY outcome

Timeframe: Study Participation of One Year

Population: Data is separately provided for the study population who were ≤75 years and those who were \>75 years old.

The prevalence of ATTR cardiac amyloidosis was calculated from among the number of subjects within the cohort determined to be ATTR-CA positive among participants ≤75 years or \>75 years enrolled in this study. Determination of ATTR was defined as significant myocardial retention of Tc-99 PYP. The prevalence is expressed as a percentage of total enrollment. ATTR-CA prevalence is reported for two different groups: Self-identified as Black, subjects with Heart Failure and Self-identified as non-Black, subjects with Heart Failure.

Outcome measures

Outcome measures
Measure
Self-identified as Black, Subjects With Heart Failure
n=550 Participants
ATTR-CA prevalence, among subjects with heart failure who self-identified as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Self-identified as Non-Black, Subjects With Heart Failure
n=96 Participants
ATTR-CA prevalence, among subjects with heart failure who did not self-identify as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Age Distribution of ATTR Cardiac Amyloidosis
Subjects ≤75 years
3.42 percentage of participants
0 percentage of participants
Age Distribution of ATTR Cardiac Amyloidosis
Subjects >75 years
14.04 percentage of participants
0 percentage of participants

PRIMARY outcome

Timeframe: Study Participation of One Year

Population: Data is separately provided for the study population who were male and those who were female.

The prevalence of ATTR cardiac amyloidosis was calculated from among the number of subjects within the cohort determined to be ATTR-CA positive among male and female participants enrolled in this study. Determination of ATTR was defined as significant myocardial retention of Tc-99 PYP. The prevalence is expressed as a percentage of total enrollment. ATTR-CA prevalence is reported for two different groups: Self-identified as Black, subjects with Heart Failure and Self-identified as non-Black, subjects with Heart Failure.

Outcome measures

Outcome measures
Measure
Self-identified as Black, Subjects With Heart Failure
n=550 Participants
ATTR-CA prevalence, among subjects with heart failure who self-identified as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Self-identified as Non-Black, Subjects With Heart Failure
n=96 Participants
ATTR-CA prevalence, among subjects with heart failure who did not self-identify as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Sex Distribution of ATTR Cardiac Amyloidosis
Percentage of female participants with ATTR
6 percentage of participants
0 percentage of participants
Sex Distribution of ATTR Cardiac Amyloidosis
Percentage of Male participants with ATTR
9.7 percentage of participants
0 percentage of participants

PRIMARY outcome

Timeframe: Study Participation of One Year

The prevalence of ATTR cardiac amyloidosis was calculated from among the number of subjects within the cohort determined to be ATTR-CA positive among those self-identified as Hispanic, enrolled in this study. Determination of ATTR was defined as significant myocardial retention of Tc-99 PYP. The prevalence is expressed as a percentage of total enrollment. ATTR-CA prevalence is reported for two different groups: Self-identified as Black, subjects with Heart Failure and Self-identified as non-Black, subjects with Heart Failure.

Outcome measures

Outcome measures
Measure
Self-identified as Black, Subjects With Heart Failure
n=90 Participants
ATTR-CA prevalence, among subjects with heart failure who self-identified as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Self-identified as Non-Black, Subjects With Heart Failure
n=96 Participants
ATTR-CA prevalence, among subjects with heart failure who did not self-identify as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Self-Identified Hispanic Ethnicity Distribution of ATTR Cardiac Amyloidosis.
4.4 percentage of participants
0 percentage of participants

PRIMARY outcome

Timeframe: Study Participation of One Year

The prevalence of ATTR cardiac amyloidosis was calculated from among the number of subjects within the cohort determined to be ATTR-CA positive among those variant (v142i) and non-variant (wild-type) participants enrolled in this study. Determination of ATTR was defined as significant myocardial retention of Tc-99 PYP. The prevalence is expressed as a percentage of total enrollment. ATTR-CA prevalence is reported for two different groups: Self-identified as Black, subjects with Heart Failure and Self-identified as non-Black, subjects with Heart Failure.

Outcome measures

Outcome measures
Measure
Self-identified as Black, Subjects With Heart Failure
n=550 Participants
ATTR-CA prevalence, among subjects with heart failure who self-identified as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
Self-identified as Non-Black, Subjects With Heart Failure
n=96 Participants
ATTR-CA prevalence, among subjects with heart failure who did not self-identify as Black, which was determined by 99mTc-PYP (or 99mTc-HDP) scintigraphy.
ATTR Type Distribution of Cardiac Amyloidosis
Subjects without v142i variant
24 Participants
0 Participants
ATTR Type Distribution of Cardiac Amyloidosis
Subjects with v142i variant
19 Participants
0 Participants

Adverse Events

Self Identified as Black, Subjects With Heart Failure

Serious events: 0 serious events
Other events: 2 other events
Deaths: 22 deaths

Self Identified as Non-Black, Subjects With Heart Failure

Serious events: 0 serious events
Other events: 0 other events
Deaths: 9 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Self Identified as Black, Subjects With Heart Failure
n=550 participants at risk
Adverse event prevalence, among subjects with heart failure who self-identified as Black, according to description above.
Self Identified as Non-Black, Subjects With Heart Failure
n=96 participants at risk
Adverse event prevalence, among subjects with heart failure who self-identified as non-Black, according to description above.
Gastrointestinal disorders
Nausea
0.18%
1/550 • Number of events 1 • One Year
Only adverse events that met the specified criteria listed in the protocol were collected. The protocol states: "In accordance with 21 CFR 312.32(a), a suspected adverse reaction (SAR) means any adverse event for which there is a reasonable possibility that the drug caused the adverse event." Therefore only events adjudged to be related to PYP administration are listed.
0.00%
0/96 • One Year
Only adverse events that met the specified criteria listed in the protocol were collected. The protocol states: "In accordance with 21 CFR 312.32(a), a suspected adverse reaction (SAR) means any adverse event for which there is a reasonable possibility that the drug caused the adverse event." Therefore only events adjudged to be related to PYP administration are listed.
General disorders
Dizziness
0.18%
1/550 • Number of events 1 • One Year
Only adverse events that met the specified criteria listed in the protocol were collected. The protocol states: "In accordance with 21 CFR 312.32(a), a suspected adverse reaction (SAR) means any adverse event for which there is a reasonable possibility that the drug caused the adverse event." Therefore only events adjudged to be related to PYP administration are listed.
0.00%
0/96 • One Year
Only adverse events that met the specified criteria listed in the protocol were collected. The protocol states: "In accordance with 21 CFR 312.32(a), a suspected adverse reaction (SAR) means any adverse event for which there is a reasonable possibility that the drug caused the adverse event." Therefore only events adjudged to be related to PYP administration are listed.

Additional Information

Mathew Maurer

Columbia University Irving Medical Center

Phone: 2123058274

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place