Trial Outcomes & Findings for MRI Study to Evaluate the Safety and Efficacy of SM04690 for Knee Osteoarthritis (NCT NCT03706521)

NCT ID: NCT03706521

Last Updated: 2026-03-04

Results Overview

The assessment of hyaline cartilage thickness present in the knee joint can be useful in evaluating cartilage health. Cartilage thickness decreases may indicate knee osteoarthritis progression. Cartilage thickness was measured using a semi-automated Local-Area Cartilage Segmentation (LACS) software for knee cartilage segmentation of knee MRI. The LACS coordinate system is based on anatomical bony landmarks and permits measurement within any subregion of the femorotibial joint consistently across longitudinal assessments.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

13 participants

Primary outcome timeframe

Baseline and Week 26

Results posted on

2026-03-04

Participant Flow

Participant milestones

Participant milestones
Measure
Lorecivivint 0.07 mg
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Overall Study
STARTED
13
Overall Study
COMPLETED
7
Overall Study
NOT COMPLETED
6

Reasons for withdrawal

Reasons for withdrawal
Measure
Lorecivivint 0.07 mg
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Overall Study
Lost to Follow-up
2
Overall Study
Physician Decision
1
Overall Study
Withdrawal by Subject
1
Overall Study
Study Closure
2

Baseline Characteristics

MRI Study to Evaluate the Safety and Efficacy of SM04690 for Knee Osteoarthritis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Lorecivivint 0.07 mg
n=13 Participants
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Age, Categorical
<=18 years
0 Participants
n=41 Participants
Age, Categorical
Between 18 and 65 years
11 Participants
n=41 Participants
Age, Categorical
>=65 years
2 Participants
n=41 Participants
Age, Continuous
56.5 years
STANDARD_DEVIATION 10.5 • n=41 Participants
Sex: Female, Male
Female
5 Participants
n=41 Participants
Sex: Female, Male
Male
8 Participants
n=41 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
1 Participants
n=41 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
12 Participants
n=41 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=41 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=41 Participants
Race (NIH/OMB)
Asian
3 Participants
n=41 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=41 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=41 Participants
Race (NIH/OMB)
White
9 Participants
n=41 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=41 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=41 Participants

PRIMARY outcome

Timeframe: Baseline and Week 26

Population: Given the impact of COVID-19 on data completeness, those subjects that were able to be measured are reported. Formal efficacy analyses were not performed due to the early termination of the study (administrative reasons). No formal Statistical Analysis Plan was prepared, and the clinical study report was finalized without completing any statistical analysis.

The assessment of hyaline cartilage thickness present in the knee joint can be useful in evaluating cartilage health. Cartilage thickness decreases may indicate knee osteoarthritis progression. Cartilage thickness was measured using a semi-automated Local-Area Cartilage Segmentation (LACS) software for knee cartilage segmentation of knee MRI. The LACS coordinate system is based on anatomical bony landmarks and permits measurement within any subregion of the femorotibial joint consistently across longitudinal assessments.

Outcome measures

Outcome measures
Measure
Lorecivivint 0.07 mg
n=6 Participants
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Change From Baseline in Medial Tibial Cartilage Thickness in the Target Knee as Measured by MRI
0.15 millimeters
Interval -0.2 to 1.0

PRIMARY outcome

Timeframe: Baseline and Week 26

Population: Given the impact of COVID-19 on data completeness, those subjects that were able to be measured are reported. Formal efficacy analyses were not performed due to the early termination of the study (administrative reasons). No formal Statistical Analysis Plan was prepared, and the clinical study report was finalized without completing any statistical analysis.

The assessment of hyaline cartilage volume present in the knee joint can be useful in evaluating cartilage health. Cartilage volume decreases may indicate knee osteoarthritis progression. Cartilage volume was measured using a semi-automated Local-Area Cartilage Segmentation (LACS) software for knee cartilage segmentation of knee MRI. The LACS coordinate system is based on anatomical bony landmarks and permits measurement within any subregion of the femorotibial joint consistently across longitudinal assessments.

Outcome measures

Outcome measures
Measure
Lorecivivint 0.07 mg
n=6 Participants
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Change From Baseline in Medial Tibial Cartilage Volume in the Target Knee as Measured by MRI
42.33 cubic millimeters
Interval -146.1 to 415.0

PRIMARY outcome

Timeframe: Baseline and Week 26

Population: Given the impact of COVID-19 on data completeness, those subjects that were able to be measured are reported. Formal efficacy analyses were not performed due to the early termination of the study (administrative reasons). No formal Statistical Analysis Plan was prepared, and the clinical study report was finalized without completing any statistical analysis.

T1rho mapping refers to an investigational magnetic resonance imaging technique that measures the low-frequency interactions between macromolecules such as proteoglycan and glycosaminoglycan and water, useful for evaluating cartilage health. Increase in T1rho measurements over time can represent cartilage degeneration.

Outcome measures

Outcome measures
Measure
Lorecivivint 0.07 mg
n=6 Participants
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Change From Baseline in Average T1 Rho for the Medial Tibial Cartilage of Target Knee
2.345 milliseconds
Interval -8.92 to 8.79

PRIMARY outcome

Timeframe: Baseline and Week 26

Population: Given the impact of COVID-19 on data completeness, those subjects that were able to be measured are reported. Formal efficacy analyses were not performed due to the early termination of the study (administrative reasons). No formal Statistical Analysis Plan was prepared, and the clinical study report was finalized without completing any statistical analysis.

T2 mapping refers to an investigational magnetic resonance imaging technique that measures biochemical changes in cartilage, including the integrity of collagen network, and collagen and water content, useful for evaluating cartilage health. Increase in T2 mapping measurements over time can represent cartilage degeneration.

Outcome measures

Outcome measures
Measure
Lorecivivint 0.07 mg
n=6 Participants
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Change From Baseline in Average T2 Mapping in Medial Tibial Cartilage of Target Knee
-0.4 milliseconds
Interval -5.48 to 4.85

Adverse Events

Lorecivivint 0.07 mg

Serious events: 0 serious events
Other events: 4 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Lorecivivint 0.07 mg
n=13 participants at risk
Single intra-articular injection of lorecivivint (SM04690) 0.07 mg in 2 mL vehicle lorecivivint: Healthcare professional-administered intra-articular injection performed once on Day 1 of the study.
Musculoskeletal and connective tissue disorders
Arthralgia
7.7%
1/13 • Number of events 1 • Adverse events were assessed at each in-person visit and phone contact from the time of study injection on Day 1 through the Week 52 (end of study).
Injury, poisoning and procedural complications
Fall
7.7%
1/13 • Number of events 1 • Adverse events were assessed at each in-person visit and phone contact from the time of study injection on Day 1 through the Week 52 (end of study).
Musculoskeletal and connective tissue disorders
Joint lock
7.7%
1/13 • Number of events 1 • Adverse events were assessed at each in-person visit and phone contact from the time of study injection on Day 1 through the Week 52 (end of study).
Infections and infestations
Nasopharyngitis
7.7%
1/13 • Number of events 1 • Adverse events were assessed at each in-person visit and phone contact from the time of study injection on Day 1 through the Week 52 (end of study).
Injury, poisoning and procedural complications
Tendon rupture
7.7%
1/13 • Number of events 1 • Adverse events were assessed at each in-person visit and phone contact from the time of study injection on Day 1 through the Week 52 (end of study).
Ear and labyrinth disorders
Vertigo
7.7%
1/13 • Number of events 1 • Adverse events were assessed at each in-person visit and phone contact from the time of study injection on Day 1 through the Week 52 (end of study).

Additional Information

Christopher Swearingen, PhD, VP of Biometrics

Biosplice Therapeutics, Inc.

Phone: 858.926.2900

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place