A RETROspective Study of Patients With TK2d
NCT03701568 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 38
Last updated 2023-09-01
Summary
This is a medical chart review study to collect information for patients who have been taking pyrimidine nucleosides for treatment of TK2 deficiency. Information from the time of onset of symptoms will be collected to describe the pre treatment course of TK2 deficiency.
Conditions
- Thymidine Kinase 2 (TK2)
Interventions
- DRUG
-
dC/dT
Collection of retrospective data from TK2 patients previously treated with dC/dT
Sponsors & Collaborators
-
Zogenix MDS, Inc.
lead INDUSTRY
Principal Investigators
-
UCB Cares · 001 844 599 2273
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2018-11-19
- Primary Completion
- 2019-04-30
- Completion
- 2019-05-31
Countries
- United States
- Israel
- Spain
Study Locations
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